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AAV-Mediated Gene Supplementation Therapy in Achromatopsia Type 2: Preclinical Data on Therapeutic Time Window and Long-Term Effects.
Mühlfriedel, Regine; Tanimoto, Naoyuki; Schön, Christian; Sothilingam, Vithiyanjali; Garcia Garrido, Marina; Beck, Susanne C; Huber, Gesine; Biel, Martin; Seeliger, Mathias W; Michalakis, Stylianos.
Affiliation
  • Mühlfriedel R; Division of Ocular Neurodegeneration, Centre for Ophthalmology, Institute for Ophthalmic Research, Eberhard Karls-Universität TübingenTuebingen, Germany.
  • Tanimoto N; Division of Ocular Neurodegeneration, Centre for Ophthalmology, Institute for Ophthalmic Research, Eberhard Karls-Universität TübingenTuebingen, Germany.
  • Schön C; Department of Pharmacy, Center for Drug Research, Center for Integrated Protein Science Munich, Ludwig-Maximilians-Universität MünchenMunich, Germany.
  • Sothilingam V; Division of Ocular Neurodegeneration, Centre for Ophthalmology, Institute for Ophthalmic Research, Eberhard Karls-Universität TübingenTuebingen, Germany.
  • Garcia Garrido M; Division of Ocular Neurodegeneration, Centre for Ophthalmology, Institute for Ophthalmic Research, Eberhard Karls-Universität TübingenTuebingen, Germany.
  • Beck SC; Division of Ocular Neurodegeneration, Centre for Ophthalmology, Institute for Ophthalmic Research, Eberhard Karls-Universität TübingenTuebingen, Germany.
  • Huber G; Division of Ocular Neurodegeneration, Centre for Ophthalmology, Institute for Ophthalmic Research, Eberhard Karls-Universität TübingenTuebingen, Germany.
  • Biel M; Department of Pharmacy, Center for Drug Research, Center for Integrated Protein Science Munich, Ludwig-Maximilians-Universität MünchenMunich, Germany.
  • Seeliger MW; Division of Ocular Neurodegeneration, Centre for Ophthalmology, Institute for Ophthalmic Research, Eberhard Karls-Universität TübingenTuebingen, Germany.
  • Michalakis S; Department of Pharmacy, Center for Drug Research, Center for Integrated Protein Science Munich, Ludwig-Maximilians-Universität MünchenMunich, Germany.
Front Neurosci ; 11: 292, 2017.
Article de En | MEDLINE | ID: mdl-28596720

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Langue: En Journal: Front Neurosci Année: 2017 Type de document: Article Pays d'affiliation: Allemagne

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Langue: En Journal: Front Neurosci Année: 2017 Type de document: Article Pays d'affiliation: Allemagne