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Clearance of Heparan Sulfate and Attenuation of CNS Pathology by Intracerebroventricular BMN 250 in Sanfilippo Type B Mice.
Aoyagi-Scharber, Mika; Crippen-Harmon, Danielle; Lawrence, Roger; Vincelette, Jon; Yogalingam, Gouri; Prill, Heather; Yip, Bryan K; Baridon, Brian; Vitelli, Catherine; Lee, Amanda; Gorostiza, Olivia; Adintori, Evan G; Minto, Wesley C; Van Vleet, Jeremy L; Yates, Bridget; Rigney, Sara; Christianson, Terri M; Tiger, Pascale M N; Lo, Melanie J; Holtzinger, John; Fitzpatrick, Paul A; LeBowitz, Jonathan H; Bullens, Sherry; Crawford, Brett E; Bunting, Stuart.
Affiliation
  • Aoyagi-Scharber M; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Crippen-Harmon D; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Lawrence R; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Vincelette J; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Yogalingam G; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Prill H; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Yip BK; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Baridon B; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Vitelli C; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Lee A; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Gorostiza O; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Adintori EG; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Minto WC; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Van Vleet JL; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Yates B; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Rigney S; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Christianson TM; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Tiger PMN; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Lo MJ; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Holtzinger J; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Fitzpatrick PA; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • LeBowitz JH; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Bullens S; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Crawford BE; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Bunting S; Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
Mol Ther Methods Clin Dev ; 6: 43-53, 2017 Sep 15.
Article de En | MEDLINE | ID: mdl-28664165

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Langue: En Journal: Mol Ther Methods Clin Dev Année: 2017 Type de document: Article Pays d'affiliation: États-Unis d'Amérique

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Langue: En Journal: Mol Ther Methods Clin Dev Année: 2017 Type de document: Article Pays d'affiliation: États-Unis d'Amérique