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Natural history study of glycan accumulation in large animal models of GM2 gangliosidoses.
Cavender, Catlyn; Mangini, Linley; Van Vleet, Jeremy L; Corado, Carley; McCullagh, Emma; Gray-Edwards, Heather L; Martin, Douglas R; Crawford, Brett E; Lawrence, Roger.
Affiliation
  • Cavender C; Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America.
  • Mangini L; Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America.
  • Van Vleet JL; Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America.
  • Corado C; Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America.
  • McCullagh E; Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America.
  • Gray-Edwards HL; University of Massachusetts Medical School, Worcester, MA, United States of America.
  • Martin DR; Scott-Ritchey Research Center and Department of Anatomy, Physiology, and Pharmacology, Auburn University College of Veterinary Medicine, Auburn, AL, United States of America.
  • Crawford BE; Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America.
  • Lawrence R; Research, BioMarin Pharmaceutical Inc., Novato, CA, United States of America.
PLoS One ; 15(12): e0243006, 2020.
Article de En | MEDLINE | ID: mdl-33259552

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Polyosides / Gangliosidoses à GM2 Type d'étude: Prognostic_studies Limites: Animals Langue: En Journal: PLoS One Sujet du journal: CIENCIA / MEDICINA Année: 2020 Type de document: Article Pays d'affiliation: États-Unis d'Amérique Pays de publication: États-Unis d'Amérique

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Polyosides / Gangliosidoses à GM2 Type d'étude: Prognostic_studies Limites: Animals Langue: En Journal: PLoS One Sujet du journal: CIENCIA / MEDICINA Année: 2020 Type de document: Article Pays d'affiliation: États-Unis d'Amérique Pays de publication: États-Unis d'Amérique