Lentivirus-mediated gene therapy for Fabry disease.

Khan, Aneal; Barber, Dwayne L; Huang, Ju; Rupar, C Anthony; Rip, Jack W; Auray-Blais, Christiane; Boutin, Michel; O'Hoski, Pamela; Gargulak, Kristy; McKillop, William M; Fraser, Graeme; Wasim, Syed; LeMoine, Kaye; Jelinski, Shelly; Chaudhry, Ahsan; Prokopishyn, Nicole; Morel, Chantal F; Couban, Stephen; Duggan, Peter R; Fowler, Daniel H; Keating, Armand; West, Michael L; Foley, Ronan; Medin, Jeffrey A

Khan, Aneal; Barber, Dwayne L; Huang, Ju; Rupar, C Anthony; Rip, Jack W; Auray-Blais, Christiane; Boutin, Michel; O'Hoski, Pamela; Gargulak, Kristy; McKillop, William M; Fraser, Graeme; Wasim, Syed; LeMoine, Kaye; Jelinski, Shelly; Chaudhry, Ahsan; Prokopishyn, Nicole; Morel, Chantal F; Couban, Stephen; Duggan, Peter R; Fowler, Daniel H; Keating, Armand; West, Michael L; Foley, Ronan; Medin, Jeffrey A.

Affiliation

Khan A; Department of Medical Genetics, Metabolics and Pediatrics, Alberta Children's Hospital, Cumming School of Medicine, Research Institute, University of Calgary, Calgary, AB, Canada.
Barber DL; University Health Network, Toronto, ON, Canada.
Huang J; Department of Laboratory Medicine and Pathobiology, University of Toronto, Toronto, ON, Canada.
Rupar CA; University Health Network, Toronto, ON, Canada.
Rip JW; Department of Pathology and Laboratory Medicine, Western University, London, ON, Canada.
Auray-Blais C; Department of Pediatrics, Western University, London, ON, Canada.
Boutin M; Children's Health Research Institute, London, ON, Canada.
O'Hoski P; Department of Pathology and Laboratory Medicine, Western University, London, ON, Canada.
Gargulak K; Division of Medical Genetics, Department of Pediatrics, CIUSSS de l'Estrie-CHUS Hospital Fleurimont, Université de Sherbrooke, Sherbrooke, QC, Canada.
McKillop WM; Division of Medical Genetics, Department of Pediatrics, CIUSSS de l'Estrie-CHUS Hospital Fleurimont, Université de Sherbrooke, Sherbrooke, QC, Canada.
Fraser G; Department of Pathology and Molecular Medicine, McMaster University and Juravinski Hospital and Cancer Centre, Hamilton, ON, Canada.
Wasim S; Department of Pediatrics, Medical College of Wisconsin, Milwaukee, WI, USA.
LeMoine K; Department of Pediatrics, Medical College of Wisconsin, Milwaukee, WI, USA.
Jelinski S; Department of Oncology, McMaster University and Juravinski Hospital and Cancer Centre, Hamilton, ON, Canada.
Chaudhry A; Cancer Clinical Research Unit, Princess Margaret Cancer Centre, Toronto, ON, Canada.
Prokopishyn N; Nova Scotia Health Authority, QEII Health Sciences Centre, Canadian Fabry Disease Initiative, Nova Scotia Fabry Disease Program, Halifax, NS, Canada.
Morel CF; Alberta Children's Hospital and Foothills Medical Centre, Calgary, AB, Canada.
Couban S; Tom Baker Cancer Centre, Alberta Health Services, Calgary, AB, Canada.
Duggan PR; Departments of Oncology and Medicine, Alberta Blood and Marrow Transplant Program, University of Calgary, Calgary, AB, Canada.
Fowler DH; Department of Pathology and Laboratory Medicine, Cumming School of Medicine, University of Calgary, Calgary, AB, Canada.
Keating A; Fred A. Litwin Family Centre in Genetic Medicine, Department of Medicine, University Health Network, Toronto, ON, Canada.
West ML; Division of Hematology, Department of Medicine, Dalhousie University, Halifax, NS, Canada.
Foley R; Cumming School of Medicine, University of Calgary, Calgary, AB, Canada.
Medin JA; Rapa Therapeutics, Rockville, MD, USA.

Nat Commun ; 12(1): 1178, 2021 02 25.

Article de En | MEDLINE | ID: mdl-33633114

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Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Thérapie génétique / Maladie de Fabry / Alpha-Galactosidase / Lentivirus Type d'étude: Clinical_trials Limites: Adult / Humans / Male / Middle aged Langue: En Journal: Nat Commun Sujet du journal: BIOLOGIA / CIENCIA Année: 2021 Type de document: Article Pays d'affiliation: Canada Pays de publication: Royaume-Uni

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