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Riociguat for the treatment of Phe508del homozygous adults with cystic fibrosis.
Derichs, Nico; Taylor-Cousar, Jennifer L; Davies, Jane C; Fajac, Isabelle; Tullis, Elizabeth; Nazareth, Dilip; Downey, Damian G; Rosenbluth, Daniel; Malfroot, Anne; Saunders, Clare; Jensen, Renee; Solomon, George M; Vermeulen, Francois; Kaiser, Andreas; Willmann, Stefan; Saleh, Soundos; Droebner, Karoline; Sandner, Peter; Bear, Christine E; Hoffmann, Anja; Ratjen, Felix; Rowe, Steven M.
Affiliation
  • Derichs N; Charité, Berlin, Germany. Electronic address: nico.derichs@me.com.
  • Taylor-Cousar JL; National Jewish Health, Denver, CO, USA. Electronic address: TaylorCousarJ@NJHealth.org.
  • Davies JC; National Heart & Lung Institute, Imperial College London and Royal Brompton Foundation Trust, London, UK. Electronic address: j.c.davies@imperial.ac.uk.
  • Fajac I; AP-HP.Centre, Université de Paris, Paris, France. Electronic address: isabelle.fajac@parisdescartes.fr.
  • Tullis E; St. Michael's Hospital, University of Toronto, Toronto, ON, Canada. Electronic address: Elizabeth.Tullis@unityhealth.to.
  • Nazareth D; Liverpool Heart and Chest Hospital, Liverpool, UK. Electronic address: Dilip.Nazareth@lhch.nhs.uk.
  • Downey DG; Wellcome-Wolfson Institute for Experimental Medicine, Queen's University Belfast, Belfast, UK. Electronic address: d.downey@qub.ac.uk.
  • Rosenbluth D; Washington University School of Medicine, St. Louis, MO, USA. Electronic address: drosenbl@dom.wustl.edu.
  • Malfroot A; Universitair Ziekenhuis Brussel, Brussels, Belgium. Electronic address: Anne.malfroot@uzbrussel.be.
  • Saunders C; National Heart & Lung Institute, Imperial College London and Royal Brompton Foundation Trust, London, UK. Electronic address: c.saunders@imperial.ac.uk.
  • Jensen R; Division of Respiratory Medicine, Department of Pediatrics, Translational Medicine, Research Institute, The Hospital for Sick Children and University of Toronto, Toronto, ON, Canada. Electronic address: renee.jensen@sickkids.ca.
  • Solomon GM; University of Alabama at Birmingham, Birmingham, AL, USA. Electronic address: gsolomon@uabmc.edu.
  • Vermeulen F; CF Reference Center, University Hospitals of Leuven, Leuven, Belgium. Electronic address: francois.vermeulen@uzleuven.be.
  • Kaiser A; Bayer AG, Berlin, Germany. Electronic address: andreas.kaiser@bayer.com.
  • Willmann S; Bayer AG, Wuppertal, Germany. Electronic address: stefan.willmann@bayer.com.
  • Saleh S; Bayer AG, Wuppertal, Germany. Electronic address: soundos.saleh@bayer.com.
  • Droebner K; Bayer AG, Wuppertal, Germany. Electronic address: karoline.droebner@bayer.com.
  • Sandner P; Bayer AG, Wuppertal, Germany. Electronic address: peter.sandner@bayer.com.
  • Bear CE; Molecular Medicine, Research Institute, The Hospital for Sick Children, Toronto, ON, Canada. Electronic address: bear@sickkids.ca.
  • Hoffmann A; Bayer AG, Berlin, Germany. Electronic address: anja.hoffmann@bayer.com.
  • Ratjen F; Division of Respiratory Medicine, Department of Pediatrics, Translational Medicine, Research Institute, The Hospital for Sick Children and University of Toronto, Toronto, ON, Canada. Electronic address: felix.ratjen@sickkids.ca.
  • Rowe SM; University of Alabama at Birmingham, Birmingham, AL, USA. Electronic address: smrowe@uab.edu.
J Cyst Fibros ; 20(6): 1018-1025, 2021 11.
Article de En | MEDLINE | ID: mdl-34419414

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Pyrazoles / Pyrimidines / Activateurs d'enzymes / Mucoviscidose Type d'étude: Clinical_trials Limites: Adult / Female / Humans / Male Langue: En Journal: J Cyst Fibros Année: 2021 Type de document: Article

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Pyrazoles / Pyrimidines / Activateurs d'enzymes / Mucoviscidose Type d'étude: Clinical_trials Limites: Adult / Female / Humans / Male Langue: En Journal: J Cyst Fibros Année: 2021 Type de document: Article