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Elexacaftor/VX-445-mediated CFTR interactome remodeling reveals differential correction driven by mutation-specific translational dynamics.
Kim, Minsoo; McDonald, Eli Fritz; Sabusap, Carleen Mae P; Timalsina, Bibek; Joshi, Disha; Hong, Jeong S; Rab, Andras; Sorscher, Eric J; Plate, Lars.
Affiliation
  • Kim M; Department of Chemistry, Vanderbilt University, Nashville, Tennessee, USA; Program in Chemical and Physical Biology, Vanderbilt University, Nashville, Tennessee, USA.
  • McDonald EF; Department of Chemistry, Vanderbilt University, Nashville, Tennessee, USA.
  • Sabusap CMP; Department of Chemistry, Vanderbilt University, Nashville, Tennessee, USA.
  • Timalsina B; Department of Chemistry, Vanderbilt University, Nashville, Tennessee, USA.
  • Joshi D; Department of Pediatrics, Emory University, Atlanta, Georgia, USA.
  • Hong JS; Department of Pediatrics, Emory University, Atlanta, Georgia, USA.
  • Rab A; Department of Pediatrics, Emory University, Atlanta, Georgia, USA.
  • Sorscher EJ; Department of Pediatrics, Emory University, Atlanta, Georgia, USA.
  • Plate L; Department of Chemistry, Vanderbilt University, Nashville, Tennessee, USA; Department of Biological Sciences, Vanderbilt University, Nashville, Tennessee, USA; Department of Pathology, Microbiology and Immunology, Vanderbilt University Medical Center, Nashville, Tennessee, USA. Electronic address: l
J Biol Chem ; 299(10): 105242, 2023 Oct.
Article de En | MEDLINE | ID: mdl-37690692

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Pyrazoles / Variation génétique / Protéine CFTR / Mucoviscidose Type d'étude: Prognostic_studies Limites: Humans Langue: En Journal: J Biol Chem Année: 2023 Type de document: Article Pays d'affiliation: États-Unis d'Amérique Pays de publication: États-Unis d'Amérique

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Pyrazoles / Variation génétique / Protéine CFTR / Mucoviscidose Type d'étude: Prognostic_studies Limites: Humans Langue: En Journal: J Biol Chem Année: 2023 Type de document: Article Pays d'affiliation: États-Unis d'Amérique Pays de publication: États-Unis d'Amérique