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Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression.
González-Martínez, Irene; Cerro-Herreros, Estefanía; Moreno, Nerea; García-Rey, Andrea; Espinosa-Espinosa, Jorge; Carrascosa-Sàez, Marc; Piqueras-Losilla, Diego; Arzumanov, Andrey; Seoane-Miraz, David; Jad, Yahya; Raz, Richard; Wood, Matthew J; Varela, Miguel A; Llamusí, Beatriz; Artero, Rubén.
Affiliation
  • González-Martínez I; University Research Institute for Biotechnology and Biomedicine (BIOTECMED), Universidad de Valencia, Valencia, Spain.
  • Cerro-Herreros E; Translational Genomics Group, INCLIVA Biomedical Research Institute, Avenue Menéndez Pelayo 4 acc, 46010 Valencia, Spain.
  • Moreno N; University Research Institute for Biotechnology and Biomedicine (BIOTECMED), Universidad de Valencia, Valencia, Spain.
  • García-Rey A; Translational Genomics Group, INCLIVA Biomedical Research Institute, Avenue Menéndez Pelayo 4 acc, 46010 Valencia, Spain.
  • Espinosa-Espinosa J; University Research Institute for Biotechnology and Biomedicine (BIOTECMED), Universidad de Valencia, Valencia, Spain.
  • Carrascosa-Sàez M; Translational Genomics Group, INCLIVA Biomedical Research Institute, Avenue Menéndez Pelayo 4 acc, 46010 Valencia, Spain.
  • Piqueras-Losilla D; University Research Institute for Biotechnology and Biomedicine (BIOTECMED), Universidad de Valencia, Valencia, Spain.
  • Arzumanov A; Translational Genomics Group, INCLIVA Biomedical Research Institute, Avenue Menéndez Pelayo 4 acc, 46010 Valencia, Spain.
  • Seoane-Miraz D; University Research Institute for Biotechnology and Biomedicine (BIOTECMED), Universidad de Valencia, Valencia, Spain.
  • Jad Y; Translational Genomics Group, INCLIVA Biomedical Research Institute, Avenue Menéndez Pelayo 4 acc, 46010 Valencia, Spain.
  • Raz R; Group of Emerging and Neglected Diseases, Ecoepidemiology and Biodiversity, Health Sciences Faculty, Universidad Internacional SEK, Quito 170521, Ecuador.
  • Wood MJ; University Research Institute for Biotechnology and Biomedicine (BIOTECMED), Universidad de Valencia, Valencia, Spain.
  • Varela MA; University Research Institute for Biotechnology and Biomedicine (BIOTECMED), Universidad de Valencia, Valencia, Spain.
  • Llamusí B; Department of Paediatrics, Institute of Developmental and Regenerative Medicine (IDRM), University of Oxford, Roosevelt Dr, Oxford OX3 7TY, UK.
  • Artero R; MDUK Oxford Neuromuscular Centre, University of Oxford, Oxford, UK.
Mol Ther Nucleic Acids ; 34: 102024, 2023 Dec 12.
Article de En | MEDLINE | ID: mdl-37744174

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Langue: En Journal: Mol Ther Nucleic Acids Année: 2023 Type de document: Article Pays d'affiliation: Espagne

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Langue: En Journal: Mol Ther Nucleic Acids Année: 2023 Type de document: Article Pays d'affiliation: Espagne