Juvenile xanthogranuloma manifesting with LCH-associated neurodegenerative disease-like radiological findings.
Pediatr Blood Cancer
; 71(7): e31043, 2024 Jul.
Article
de En
| MEDLINE
| ID: mdl-38679849
ABSTRACT
Here, we describe two patients with juvenile xanthogranuloma (JXG) manifesting with Langerhans cell histiocytosis (LCH)-associated neurodegenerative disease (ND)-like radiological findings. One patient showed typical radiological abnormalities at onset, which worsened with progressing central nervous system symptoms 7 years after LCH-oriented chemotherapy. Another showed spontaneous regression of clinical symptoms, with a transient radiological change 1 year after salvage chemotherapy for recurrence of JXG. These data regarding JXG-associated ND will facilitate future investigation of the disease, as well as development of therapeutic interventions.
Mots clés
Texte intégral:
1
Collection:
01-internacional
Base de données:
MEDLINE
Sujet principal:
Histiocytose à cellules de Langerhans
/
Xanthome juvénile
/
Maladies neurodégénératives
Limites:
Child
/
Humans
/
Infant
/
Male
Langue:
En
Journal:
Pediatr Blood Cancer
/
Pediatr. blood cancer
/
Pediatric blood & cancer
Sujet du journal:
HEMATOLOGIA
/
NEOPLASIAS
/
PEDIATRIA
Année:
2024
Type de document:
Article
Pays d'affiliation:
Japon
Pays de publication:
États-Unis d'Amérique