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A Randomized Controlled Clinical Trial Testing Effects of Lademirsen on Kidney Function Decline in Adults with Alport Syndrome.
Gale, Daniel P; Gross, Oliver; Wang, Fang; Esteban de la Rosa, Rafael José; Hall, Matthew; Sayer, John A; Appel, Gerald; Hariri, Ali; Liu, Shiguang; Maski, Manish; Shen, Yuqian; Zhang, Qi; Iqbal, Sajida; Kowthalam, Madhurima Uppara; Lin, Julie; Ding, Jie.
Affiliation
  • Gale DP; Department of Renal Medicine, University College London, London, United Kingdom.
  • Gross O; Royal Free Hospital London, London, United Kingdom.
  • Wang F; Great Ormond Street Hospital, London, United Kingdom.
  • Esteban de la Rosa RJ; Clinic for Nephrology and Rheumatology, University Medicine Göttingen, Göttingen, Germany.
  • Hall M; Department of Pediatrics, Peking University First Hospital, Beijing, China.
  • Sayer JA; Hospital Universitario Virgen de las Nieves, University of Granada, IBS-Granada, Granada, Spain.
  • Appel G; Nottingham University Hospitals, Nottingham, United Kingdom.
  • Hariri A; Translational and Clinical Research Institute, University of Newcastle upon Tyne, Newcastle upon Tyne, United Kingdom.
  • Liu S; Columbia University Medical Center, New York, New York.
  • Maski M; Eloxx Pharmaceuticals, Watertown, Massachusetts.
  • Shen Y; Sanofi, Cambridge, Massachusetts.
  • Zhang Q; Sanofi, Cambridge, Massachusetts.
  • Iqbal S; Sanofi, Cambridge, Massachusetts.
  • Kowthalam MU; Sanofi, Cambridge, Massachusetts.
  • Lin J; Sanofi, Cambridge, Massachusetts.
  • Ding J; Sanofi, Bridgewater, New Jersey.
Clin J Am Soc Nephrol ; 19(8): 995-1004, 2024 Aug 01.
Article de En | MEDLINE | ID: mdl-38829703

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Néphropathie familiale avec surdité Limites: Adult / Female / Humans / Male / Middle aged Langue: En Journal: Clin J Am Soc Nephrol Sujet du journal: NEFROLOGIA Année: 2024 Type de document: Article Pays d'affiliation: Royaume-Uni Pays de publication: États-Unis d'Amérique

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Néphropathie familiale avec surdité Limites: Adult / Female / Humans / Male / Middle aged Langue: En Journal: Clin J Am Soc Nephrol Sujet du journal: NEFROLOGIA Année: 2024 Type de document: Article Pays d'affiliation: Royaume-Uni Pays de publication: États-Unis d'Amérique