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Outcome measures for hereditary spastic paraplegia clinical trials: Learnings from an Australian HSP center.
Siow, Sue Faye; Waters, Amy; Coward, Sharon; Wali, Gautam; Ng, Karl; Sue, Carolyn M; Kumar, Kishore R.
Affiliation
  • Siow SF; Department of Clinical Genetics, Royal North Shore Hospital, NSW, Australia; Sydney Medical School, The University of Sydney, NSW, Australia; Department of Neurogenetics, Royal North Shore Hospital, NSW, Australia. Electronic address: Suefaye.siow@health.nsw.gov.au.
  • Waters A; Department of Neurology and Clinical Neurophysiology, Royal North Shore Hospital, NSW, Australia.
  • Coward S; Department of Neurology and Clinical Neurophysiology, Royal North Shore Hospital, NSW, Australia.
  • Wali G; Sydney Medical School, The University of Sydney, NSW, Australia; Department of Neurogenetics, Royal North Shore Hospital, NSW, Australia; Neuroscience Research Australia, University of New South Wales, NSW, Australia.
  • Ng K; Sydney Medical School, The University of Sydney, NSW, Australia; Department of Neurology and Clinical Neurophysiology, Royal North Shore Hospital, NSW, Australia.
  • Sue CM; Department of Neurogenetics, Royal North Shore Hospital, NSW, Australia; Neuroscience Research Australia, University of New South Wales, NSW, Australia; Faculty of Medicine and Health, University of New South Wales Sydney, NSW, Australia.
  • Kumar KR; Sydney Medical School, The University of Sydney, NSW, Australia; Translational Neurogenomics Group, Genomics and Inherited Disease Program, Garvan Institute of Medical Research, NSW, Australia; Molecular Medicine Laboratory and Department of Neurology, Concord Repatriation General Hospital, NSW, Aus
J Neurol Sci ; 462: 123100, 2024 Jul 15.
Article de En | MEDLINE | ID: mdl-38914513

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Paraplégie spasmodique héréditaire Limites: Humans Pays/Région comme sujet: Oceania Langue: En Journal: J Neurol Sci Année: 2024 Type de document: Article Pays de publication: Pays-Bas

Texte intégral: 1 Collection: 01-internacional Base de données: MEDLINE Sujet principal: Paraplégie spasmodique héréditaire Limites: Humans Pays/Région comme sujet: Oceania Langue: En Journal: J Neurol Sci Année: 2024 Type de document: Article Pays de publication: Pays-Bas