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Restoration of muscle functionality by genetic suppression of glycogen synthesis in a murine model of Pompe disease.
Douillard-Guilloux, Gaelle; Raben, Nina; Takikita, Shoichi; Ferry, Arnaud; Vignaud, Alban; Guillet-Deniau, Isabelle; Favier, Maryline; Thurberg, Beth L; Roach, Peter J; Caillaud, Catherine; Richard, Emmanuel.
Affiliation
  • Douillard-Guilloux G; Institut Cochin, Université Paris Descartes, CNRS (UMR 8104), Paris, France.
Hum Mol Genet ; 19(4): 684-96, 2010 Feb 15.
Article in En | MEDLINE | ID: mdl-19959526

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease Type II / Muscle, Skeletal / Glycogen Type of study: Prognostic_studies Limits: Animals / Female / Humans / Male Language: En Journal: Hum Mol Genet Journal subject: BIOLOGIA MOLECULAR / GENETICA MEDICA Year: 2010 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease Type II / Muscle, Skeletal / Glycogen Type of study: Prognostic_studies Limits: Animals / Female / Humans / Male Language: En Journal: Hum Mol Genet Journal subject: BIOLOGIA MOLECULAR / GENETICA MEDICA Year: 2010 Document type: Article Affiliation country: Country of publication: