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Brain Nat8l Knockdown Suppresses Spongiform Leukodystrophy in an Aspartoacylase-Deficient Canavan Disease Mouse Model.
Bannerman, Peter; Guo, Fuzheng; Chechneva, Olga; Burns, Travis; Zhu, Xiaoqing; Wang, Yan; Kim, Bokyung; Singhal, Naveen K; McDonough, Jennifer A; Pleasure, David.
Affiliation
  • Bannerman P; Institute for Pediatric Regenerative Medicine, University of California, Davis, Sacramento, CA 95817, USA.
  • Guo F; Institute for Pediatric Regenerative Medicine, University of California, Davis, Sacramento, CA 95817, USA.
  • Chechneva O; Institute for Pediatric Regenerative Medicine, University of California, Davis, Sacramento, CA 95817, USA.
  • Burns T; Institute for Pediatric Regenerative Medicine, University of California, Davis, Sacramento, CA 95817, USA.
  • Zhu X; Cancer Institute, The Affiliated Hospital of Qingdao University, Qingdao, Shandong 266-61, China.
  • Wang Y; Institute for Pediatric Regenerative Medicine, University of California, Davis, Sacramento, CA 95817, USA.
  • Kim B; Institute for Pediatric Regenerative Medicine, University of California, Davis, Sacramento, CA 95817, USA.
  • Singhal NK; Department of Biological Sciences and School of Biomedical Sciences, Kent State University, Kent, OH 44242, USA.
  • McDonough JA; Department of Biological Sciences and School of Biomedical Sciences, Kent State University, Kent, OH 44242, USA.
  • Pleasure D; Institute for Pediatric Regenerative Medicine, University of California, Davis, Sacramento, CA 95817, USA. Electronic address: depleasure@ucdavis.edu.
Mol Ther ; 26(3): 793-800, 2018 03 07.
Article in En | MEDLINE | ID: mdl-29456021

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Acetyltransferases / Canavan Disease / Amidohydrolases Limits: Animals Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2018 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Acetyltransferases / Canavan Disease / Amidohydrolases Limits: Animals Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2018 Document type: Article Affiliation country: Country of publication: