Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis.
N Engl J Med
; 379(1): 22-31, 2018 Jul 05.
Article
in En
| MEDLINE
| ID: mdl-29972757
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Prealbumin
/
Oligonucleotides, Antisense
/
Amyloid Neuropathies, Familial
/
RNAi Therapeutics
Type of study:
Clinical_trials
/
Etiology_studies
Aspects:
Patient_preference
Limits:
Adult
/
Aged
/
Aged80
/
Female
/
Humans
/
Male
/
Middle aged
Language:
En
Journal:
N Engl J Med
Year:
2018
Document type:
Article
Country of publication: