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Luspatercept improves hemoglobin levels and blood transfusion requirements in a study of patients with ß-thalassemia.
Piga, Antonio; Perrotta, Silverio; Gamberini, Maria Rita; Voskaridou, Ersi; Melpignano, Angela; Filosa, Aldo; Caruso, Vincenzo; Pietrangelo, Antonello; Longo, Filomena; Tartaglione, Immacolata; Borgna-Pignatti, Caterina; Zhang, Xiaosha; Laadem, Abderrahmane; Sherman, Matthew L; Attie, Kenneth M.
Affiliation
  • Piga A; Department of Clinical and Biological Sciences, Turin University, Turin, Italy.
  • Perrotta S; Dipartimento della Donna, del Bambino e della Chirurgia Generale e Specialistica, Università degli Studi della Campania "Luigi Vanvitelli," Naples, Italy.
  • Gamberini MR; Thalassemia Unit, Arcispedale S. Anna, Ferrara, Italy.
  • Voskaridou E; Laiko General Hospital, Athens, Greece.
  • Melpignano A; Ospedale "A. Perrino," Brindisi, Italy.
  • Filosa A; Rare Red Blood Cell Disease Unit, Cardarelli Hospital, Naples, Italy.
  • Caruso V; Azienda Ospedaliera di Rilievo Nazionale e di Alta Specializzazione Garibaldi, Catania, Italy.
  • Pietrangelo A; Centro Emocromatosi e Malattie Eredometaboliche del Fegato, Medicina 2, Modena, Italy.
  • Longo F; Department of Clinical and Biological Sciences, Turin University, Turin, Italy.
  • Tartaglione I; Dipartimento della Donna, del Bambino e della Chirurgia Generale e Specialistica, Università degli Studi della Campania "Luigi Vanvitelli," Naples, Italy.
  • Borgna-Pignatti C; Section of Pediatrics, Department of Medical Sciences, University of Ferrara, Ferrara, Italy.
  • Zhang X; Acceleron Pharma, Cambridge, MA; and.
  • Laadem A; Celgene Corporation, Summit, NJ.
  • Sherman ML; Acceleron Pharma, Cambridge, MA; and.
  • Attie KM; Acceleron Pharma, Cambridge, MA; and.
Blood ; 133(12): 1279-1289, 2019 03 21.
Article in En | MEDLINE | ID: mdl-30617198

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Recombinant Fusion Proteins / Hemoglobins / Immunoglobulin Fc Fragments / Beta-Thalassemia / Erythrocyte Transfusion / Activins Type of study: Clinical_trials / Observational_studies / Prognostic_studies Limits: Adult / Female / Humans / Male / Middle aged Language: En Journal: Blood Year: 2019 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Recombinant Fusion Proteins / Hemoglobins / Immunoglobulin Fc Fragments / Beta-Thalassemia / Erythrocyte Transfusion / Activins Type of study: Clinical_trials / Observational_studies / Prognostic_studies Limits: Adult / Female / Humans / Male / Middle aged Language: En Journal: Blood Year: 2019 Document type: Article Affiliation country: Country of publication: