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Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency.
Magnani, Alessandra; Jouannic, Jean-Marie; Rosain, Jérémie; Gabrion, Aurélie; Touzot, Fabien; Roudaut, Cécile; Kracker, Sven; Mahlaoui, Nizar; Toubert, Antoine; Clave, Emmanuel; Macintyre, Elisabeth A; Radford-Weiss, Isabelle; Alcantara, Marion; Magrin, Elisa; Ternaux, Brigitte; Nisoy, Jennifer; Caccavelli, Laure; Darras, Anne-Marie; Picard, Capucine; Blanche, Stéphane; Cavazzana, Marina.
Affiliation
  • Magnani A; Department of Biotherapy, Necker-Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Jouannic JM; Laboratory of Human Lymphohematopoiesis, INSERM Unité Mixte de Recherche (UMR) 1163, Imagine Institute, Paris, France.
  • Rosain J; Department of Fetal Medicine, Armand Trousseau Hospital, Assistance Publique-Hôpitaux de Paris, Sorbonne University, Paris, France.
  • Gabrion A; Study Center for Primary Immunodeficiencies, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.
  • Touzot F; Paris Descartes-Sorbonne Paris Cité University, Imagine Institute, Paris, France.
  • Roudaut C; Department of Biotherapy, Necker-Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Kracker S; Laboratory of Human Lymphohematopoiesis, INSERM Unité Mixte de Recherche (UMR) 1163, Imagine Institute, Paris, France.
  • Mahlaoui N; Department of Immunology-Allergy-Rheumatology, Centre Hospitalier Universitaire Sainte-Justine, University of Montreal, Montreal, QC, Canada.
  • Toubert A; Department of Biotherapy, Necker-Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Clave E; Laboratory of Human Lymphohematopoiesis, INSERM Unité Mixte de Recherche (UMR) 1163, Imagine Institute, Paris, France.
  • Macintyre EA; Laboratory of Human Lymphohematopoiesis, INSERM Unité Mixte de Recherche (UMR) 1163, Imagine Institute, Paris, France.
  • Radford-Weiss I; Paris Descartes-Sorbonne Paris Cité University, Imagine Institute, Paris, France.
  • Alcantara M; Department of Pediatric Immunology, Hematology and Rheumatology, Necker-Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Magrin E; French National Reference Center for Primary Immune Deficiencies, Necker-Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Ternaux B; Université Paris Diderot, Sorbonne Paris Cité, Institut Universitaire d'Hématologie, Paris, France.
  • Nisoy J; INSERM UMR1160, Alloimmunity-Autoimmunity-Transplantation, Paris, France.
  • Caccavelli L; Laboratoire d'Immunologie et d'Histocompatibilité, Hôpital Saint-Louis, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Darras AM; Université Paris Diderot, Sorbonne Paris Cité, Institut Universitaire d'Hématologie, Paris, France.
  • Picard C; INSERM UMR1160, Alloimmunity-Autoimmunity-Transplantation, Paris, France.
  • Blanche S; Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, INSERM U1151, Paris, France.
  • Cavazzana M; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.
Blood Adv ; 3(3): 237-241, 2019 02 12.
Article in En | MEDLINE | ID: mdl-30683657

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hematopoietic Stem Cell Transplantation / Transplantation Conditioning / X-Linked Combined Immunodeficiency Diseases Limits: Child, preschool / Female / Humans Language: En Journal: Blood Adv Year: 2019 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hematopoietic Stem Cell Transplantation / Transplantation Conditioning / X-Linked Combined Immunodeficiency Diseases Limits: Child, preschool / Female / Humans Language: En Journal: Blood Adv Year: 2019 Document type: Article Affiliation country: Country of publication: