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Predictive model of response to tafamidis in hereditary ATTR polyneuropathy.
Monteiro, Cecília; Mesgazardeh, Jaleh S; Anselmo, João; Fernandes, Joana; Novais, Marta; Rodrigues, Carla; Brighty, Gabriel J; Powers, David L; Powers, Evan T; Coelho, Teresa; Kelly, Jeffery W.
Affiliation
  • Monteiro C; Departments of Chemistry and Molecular Medicine, The Scripps Research Institute, La Jolla, California, USA.
  • Mesgazardeh JS; Departments of Chemistry and Molecular Medicine, The Scripps Research Institute, La Jolla, California, USA.
  • Anselmo J; Unidade Corino de Andrade, Centro Hospitalar do Porto, Porto, Portugal.
  • Fernandes J; Unidade Corino de Andrade, Centro Hospitalar do Porto, Porto, Portugal.
  • Novais M; Unidade Corino de Andrade, Centro Hospitalar do Porto, Porto, Portugal.
  • Rodrigues C; Unidade Corino de Andrade, Centro Hospitalar do Porto, Porto, Portugal.
  • Brighty GJ; Departments of Chemistry and Molecular Medicine, The Scripps Research Institute, La Jolla, California, USA.
  • Powers DL; Department of Mathematics, Clarkson University, Potsdam, New York, USA.
  • Powers ET; Departments of Chemistry and Molecular Medicine, The Scripps Research Institute, La Jolla, California, USA.
  • Coelho T; Unidade Corino de Andrade, Centro Hospitalar do Porto, Porto, Portugal.
  • Kelly JW; Department of Neurophysiology, Centro Hospitalar do Porto, Porto, Portugal.
JCI Insight ; 4(12)2019 06 20.
Article in En | MEDLINE | ID: mdl-31217346

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Benzoxazoles / Amyloid Neuropathies, Familial Type of study: Etiology_studies / Incidence_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Adult / Aged / Aged80 / Female / Humans / Male / Middle aged Language: En Journal: JCI Insight Year: 2019 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Benzoxazoles / Amyloid Neuropathies, Familial Type of study: Etiology_studies / Incidence_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Adult / Aged / Aged80 / Female / Humans / Male / Middle aged Language: En Journal: JCI Insight Year: 2019 Document type: Article Affiliation country: Country of publication: