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Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on In Vitro Experimental Evidence.
Huang, Yunjie; Paul, Grace; Lee, Jesun; Yarlagadda, Sunitha; McCoy, Karen; Naren, Anjaparavanda P.
Affiliation
  • Huang Y; Cincinnati Children's Hospital Medical Center Cincinnati, Ohio.
  • Paul G; Nationwide Children's Hospital Columbus, Ohio.
  • Lee J; Cincinnati Children's Hospital Medical Center Cincinnati, Ohio.
  • Yarlagadda S; Cincinnati Children's Hospital Medical Center Cincinnati, Ohio.
  • McCoy K; Nationwide Children's Hospital Columbus, Ohio.
  • Naren AP; Cincinnati Children's Hospital Medical Center Cincinnati, Ohio.
Am J Respir Crit Care Med ; 204(10): 1231-1235, 2021 11 15.
Article in En | MEDLINE | ID: mdl-34379998

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Gene Expression Regulation / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Drug Combinations / Mutation Limits: Adolescent / Adult / Aged / Aged80 / Child / Female / Humans / Male / Middle aged Language: En Journal: Am J Respir Crit Care Med Journal subject: TERAPIA INTENSIVA Year: 2021 Document type: Article Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Gene Expression Regulation / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Drug Combinations / Mutation Limits: Adolescent / Adult / Aged / Aged80 / Child / Female / Humans / Male / Middle aged Language: En Journal: Am J Respir Crit Care Med Journal subject: TERAPIA INTENSIVA Year: 2021 Document type: Article Country of publication: