Use of pegvaliase in the management of phenylketonuria: Case series of early experience in US clinics.
Mol Genet Metab Rep
; 28: 100790, 2021 Sep.
Article
in En
| MEDLINE
| ID: mdl-34430209
ACMG, American College of Medical Genetics and Genomics; AEs, adverse events; Adverse events; BH4, tetrahydrobiopterin; Case series; HCP, healthcare provider; I/T/M, induction, titration, and maintenance; PAH, phenylalanine hydroxylase; PEGylated phenylalanine ammonia lyase; PKU diet; PKU, phenylketonuria; Pegvaliase; Phe, phenylalanine; Phenylketonuria
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1
Collection:
01-internacional
Database:
MEDLINE
Language:
En
Journal:
Mol Genet Metab Rep
Year:
2021
Document type:
Article
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