Intrathecal idursulfase-IT in patients with neuronopathic mucopolysaccharidosis II: Results from a phase 2/3 randomized study.
Mol Genet Metab
; 137(1-2): 127-139, 2022.
Article
in En
| MEDLINE
| ID: mdl-36027721
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Mucopolysaccharidosis II
/
Iduronate Sulfatase
/
Multiple Myeloma
Type of study:
Clinical_trials
Limits:
Child
/
Child, preschool
/
Humans
Language:
En
Journal:
Mol Genet Metab
Journal subject:
BIOLOGIA MOLECULAR
/
BIOQUIMICA
/
METABOLISMO
Year:
2022
Document type:
Article
Country of publication: