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Lorlatinib with or without chemotherapy in ALK-driven refractory/relapsed neuroblastoma: phase 1 trial results.
Goldsmith, Kelly C; Park, Julie R; Kayser, Kimberly; Malvar, Jemily; Chi, Yueh-Yun; Groshen, Susan G; Villablanca, Judith G; Krytska, Kateryna; Lai, Lillian M; Acharya, Patricia T; Goodarzian, Fariba; Pawel, Bruce; Shimada, Hiroyuki; Ghazarian, Susan; States, Lisa; Marshall, Lynley; Chesler, Louis; Granger, Meaghan; Desai, Ami V; Mody, Rajen; Morgenstern, Daniel A; Shusterman, Suzanne; Macy, Margaret E; Pinto, Navin; Schleiermacher, Gudrun; Vo, Kieuhoa; Thurm, Holger C; Chen, Joseph; Liyanage, Marlon; Peltz, Gerson; Matthay, Katherine K; Berko, Esther R; Maris, John M; Marachelian, Araz; Mossé, Yael P.
Affiliation
  • Goldsmith KC; Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, Atlanta, GA, USA.
  • Park JR; Winship Cancer Institute, Emory University School of Medicine, Atlanta, GA, USA.
  • Kayser K; Seattle Children's Hospital, Seattle, WA, USA.
  • Malvar J; Department of Pediatrics, University of Washington School of Medicine, Seattle, WA, USA.
  • Chi YY; Department of Psychiatry and Behavioral Sciences, Vanderbilt University Medical Center, Nashville, TN, USA.
  • Groshen SG; Cancer and Blood Disease Institute, Children's Hospital Los Angeles, Los Angeles, CA, USA.
  • Villablanca JG; Cancer and Blood Disease Institute, Children's Hospital Los Angeles, Los Angeles, CA, USA.
  • Krytska K; Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Lai LM; Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Acharya PT; Cancer and Blood Disease Institute, Children's Hospital Los Angeles, Los Angeles, CA, USA.
  • Goodarzian F; Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Pawel B; Division of Oncology and Center for Childhood Cancer Research, Children's Hospital of Philadelphia, Philadelphia, PA, USA.
  • Shimada H; Department of Radiology, University of Iowa Hospital and Clinics, Iowa City, IA, USA.
  • Ghazarian S; Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • States L; Department of Radiology, Children's Hospital Los Angeles, Los Angeles, CA, USA.
  • Marshall L; Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Chesler L; Department of Radiology, Children's Hospital Los Angeles, Los Angeles, CA, USA.
  • Granger M; Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Desai AV; Department of Pathology and Laboratory Medicine, Children's Hospital Los Angeles, Los Angeles, CA, USA.
  • Mody R; Department of Pathology and Pediatrics, Stanford University School of Medicine, Stanford, CA, USA.
  • Morgenstern DA; Cancer and Blood Disease Institute, Children's Hospital Los Angeles, Los Angeles, CA, USA.
  • Shusterman S; Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA, USA.
  • Macy ME; The Royal Marsden Hospital, London, UK.
  • Pinto N; The Institute of Cancer Research, London, UK.
  • Schleiermacher G; The Royal Marsden Hospital, London, UK.
  • Vo K; The Institute of Cancer Research, London, UK.
  • Thurm HC; Cook Children's Medical Center, Fort Worth, TX, USA.
  • Chen J; Department of Pediatrics, Section of Hematology/Oncology/Stem Cell Transplantation, University of Chicago, Chicago, IL, USA.
  • Liyanage M; Department of Pediatrics, University of Michigan, Ann Arbor, MI, USA.
  • Peltz G; Division of Haematology and Oncology, Hospital for Sick Children, Toronto, ON, Canada.
  • Matthay KK; Department of Paediatrics, University of Toronto, Toronto, ON, Canada.
  • Berko ER; Dana-Farber Cancer Institute, Boston Children's Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA, USA.
  • Maris JM; University of Colorado Anschutz Medical Campus, Aurora, CO, USA.
  • Marachelian A; Center for Cancer and Blood Disorders, Children's Hospital Colorado, Aurora, CO, USA.
  • Mossé YP; Seattle Children's Hospital, Seattle, WA, USA.
Nat Med ; 29(5): 1092-1102, 2023 05.
Article in En | MEDLINE | ID: mdl-37012551

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Carcinoma, Non-Small-Cell Lung / Lung Neoplasms / Neuroblastoma Limits: Adolescent / Adult / Child / Child, preschool / Humans / Infant Language: En Journal: Nat Med Journal subject: BIOLOGIA MOLECULAR / MEDICINA Year: 2023 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Carcinoma, Non-Small-Cell Lung / Lung Neoplasms / Neuroblastoma Limits: Adolescent / Adult / Child / Child, preschool / Humans / Infant Language: En Journal: Nat Med Journal subject: BIOLOGIA MOLECULAR / MEDICINA Year: 2023 Document type: Article Affiliation country: Country of publication: