Treatment of SMA type 1 infants using a single-dose AAV9-mediated gene therapy via intrathecal injection of GC101: An open-label, single-arm study.
Chin Med J (Engl)
; 137(16): 1976-1978, 2024 Aug 20.
Article
in En
| MEDLINE
| ID: mdl-39030070
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Injections, Spinal
/
Genetic Therapy
/
Spinal Muscular Atrophies of Childhood
/
Dependovirus
Limits:
Female
/
Humans
/
Infant
/
Male
Language:
En
Journal:
Chin Med J (Engl)
Year:
2024
Document type:
Article
Affiliation country:
Country of publication: