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AAV9 Edits Muscle Stem Cells in Normal and Dystrophic Adult Mice.
Nance, Michael E; Shi, Ruicheng; Hakim, Chady H; Wasala, Nalinda B; Yue, Yongping; Pan, Xiufang; Zhang, Tracy; Robinson, Carolyn A; Duan, Sean X; Yao, Gang; Yang, N Nora; Chen, Shi-Jie; Wagner, Kathryn R; Gersbach, Charles A; Duan, Dongsheng.
Afiliação
  • Nance ME; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA.
  • Shi R; Department of Biomedical, Biological and Chemical Engineering, College of Engineering, University of Missouri, Columbia, MO 65212, USA.
  • Hakim CH; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA; National Center for Advancing Translational Sciences, NIH, Rockville, MD 20850, USA.
  • Wasala NB; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA.
  • Yue Y; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA.
  • Pan X; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA.
  • Zhang T; The Hugo W. Moser Research Institute, Kennedy Krieger Institute, Baltimore, MD 21205, USA; Department of Neurology and Neuroscience, Johns Hopkins School of Medicine, Baltimore, MD 21205, USA.
  • Robinson CA; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA.
  • Duan SX; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA.
  • Yao G; Department of Biomedical, Biological and Chemical Engineering, College of Engineering, University of Missouri, Columbia, MO 65212, USA.
  • Yang NN; National Center for Advancing Translational Sciences, NIH, Rockville, MD 20850, USA.
  • Chen SJ; Department of Physics, University of Missouri, Columbia, MO 65212, USA.
  • Wagner KR; The Hugo W. Moser Research Institute, Kennedy Krieger Institute, Baltimore, MD 21205, USA; Department of Neurology and Neuroscience, Johns Hopkins School of Medicine, Baltimore, MD 21205, USA.
  • Gersbach CA; Department of Biomedical Engineering, Duke University, Durham, NC 27708, USA.
  • Duan D; Department of Molecular Microbiology and Immunology, School of Medicine, University of Missouri, Columbia, MO 65212, USA; Department of Biomedical, Biological and Chemical Engineering, College of Engineering, University of Missouri, Columbia, MO 65212, USA; Department of Biomedical Sciences, College
Mol Ther ; 27(9): 1568-1585, 2019 09 04.
Article em En | MEDLINE | ID: mdl-31327755

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Distrofina / Dependovirus / Mioblastos / Edição de Genes / Vetores Genéticos Limite: Animals Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Distrofina / Dependovirus / Mioblastos / Edição de Genes / Vetores Genéticos Limite: Animals Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos País de publicação: Estados Unidos