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Efficacy of exon-skipping therapy for DMD cardiomyopathy with mutations in actin binding domain 1.
Shiba, Naoko; Yang, Xiao; Sato, Mitsuto; Kadota, Shin; Suzuki, Yota; Agata, Masahiro; Nagamine, Kohei; Izumi, Masaki; Honda, Yusuke; Koganehira, Tomoya; Kobayashi, Hideki; Ichimura, Hajime; Chuma, Shinichiro; Nakai, Junichi; Tohyama, Shugo; Fukuda, Keiichi; Miyazaki, Daigo; Nakamura, Akinori; Shiba, Yuji.
Afiliação
  • Shiba N; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Yang X; Department of Pediatrics, Shinshu University, Matsumoto 390-8621, Japan.
  • Sato M; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Kadota S; Department of Medicine (Neurology and Rheumatology), Shinshu University School of Medicine, Matsumoto 390-8621, Japan.
  • Suzuki Y; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Agata M; Institute for Biomedical Sciences, Shinshu University, Matsumoto 390-8621, Japan.
  • Nagamine K; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Izumi M; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Honda Y; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Koganehira T; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Kobayashi H; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Ichimura H; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Chuma S; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Nakai J; Department of Regenerative Science and Medicine, Shinshu University, Matsumoto 390-8621, Japan.
  • Tohyama S; Department of Regeneration Science and Engineering, Institute for Life and Medical Sciences, Kyoto University, Kyoto 606-8507, Japan.
  • Fukuda K; Graduate Schools of Dentistry, Tohoku University, Sendai 980-8575, Japan.
  • Miyazaki D; Department of Cardiology, Keio University School of Medicine, Tokyo 160-8582, Japan.
  • Nakamura A; Department of Cardiology, Keio University School of Medicine, Tokyo 160-8582, Japan.
  • Shiba Y; Department of Medicine (Neurology and Rheumatology), Shinshu University School of Medicine, Matsumoto 390-8621, Japan.
Mol Ther Nucleic Acids ; 34: 102060, 2023 Dec 12.
Article em En | MEDLINE | ID: mdl-38028197

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Japão País de publicação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Japão País de publicação: Estados Unidos