Detalhe da pesquisa
1.
CRISPR-Cas9 Editing of the HBG1 and HBG2 Promoters to Treat Sickle Cell Disease.
N Engl J Med
; 389(9): 820-832, 2023 Aug 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-37646679
2.
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome.
N Engl J Med
; 385(21): 1929-1940, 2021 11 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-34788506
3.
Early intestinal microbial features are associated with CD4 T-cell recovery after allogeneic hematopoietic transplant.
Blood
; 139(18): 2758-2769, 2022 05 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-35061893
4.
High-dose individualized antithymocyte globulin with therapeutic drug monitoring in high-risk cord blood transplant.
Cytotherapy
; 2024 Feb 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-38466262
5.
Impact of rabbit anti-thymocyte globulin (ATG) exposure on outcomes after ex vivo T-cell-depleted hematopoietic cell transplantation in pediatric and young adult patients.
Cytotherapy
; 26(4): 351-359, 2024 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-38349310
6.
Two novel assays demonstrate persistent daratumumab exposure in a pediatric patient with delayed engraftment following allogeneic hematopoietic stem cell transplantation.
Cytotherapy
; 26(5): 466-471, 2024 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-38430078
7.
Strategic infection prevention after genetically modified hematopoietic stem cell therapies: recommendations from the International Society for Cell & Gene Therapy Stem Cell Engineering Committee.
Cytotherapy
; 2024 Feb 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-38483362
8.
Consensus guidelines for the monitoring and management of metachromatic leukodystrophy in the United States.
Cytotherapy
; 2024 Apr 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-38613540
9.
CD4+ T-cell reconstitution predicts survival outcomes after acute graft-versus-host-disease: a dual-center validation.
Blood
; 137(6): 848-855, 2021 02 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-33150379
10.
Transplant for non-malignant disorders: an International Society for Cell & Gene Therapy Stem Cell Engineering Committee report on the role of alternative donors, stem cell sources and graft engineering.
Cytotherapy
; 25(5): 463-471, 2023 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-36710227
11.
Engineering the best transplant outcome for high-risk acute myeloid leukemia: the donor, the graft and beyond.
Cytotherapy
; 2023 Dec 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-38054912
12.
Early immune reconstitution as predictor for outcomes after allogeneic hematopoietic cell transplant; a tri-institutional analysis.
Cytotherapy
; 25(9): 977-985, 2023 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-37330731
13.
International Society for Cell & Gene Therapy Stem Cell Engineering Committee: Cellular therapies for the treatment of graft-versus-host-disease after hematopoietic stem cell transplant.
Cytotherapy
; 25(6): 578-589, 2023 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-36941149
14.
Neurofilament light chain and glial fibrillary acidic protein levels in metachromatic leukodystrophy.
Brain
; 145(1): 105-118, 2022 03 29.
Artigo
em Inglês
| MEDLINE | ID: mdl-34398223
15.
Curative therapy for hemoglobinopathies: an International Society for Cell & Gene Therapy Stem Cell Engineering Committee review comparing outcomes, accessibility and cost of ex vivo stem cell gene therapy versus allogeneic hematopoietic stem cell transplantation.
Cytotherapy
; 24(3): 249-261, 2022 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34879990
16.
An ISCT Stem Cell Engineering Committee Position Statement on Immune Reconstitution: the importance of predictable and modifiable milestones of immune reconstitution to transplant outcomes.
Cytotherapy
; 24(4): 385-392, 2022 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-35331394
17.
Time to initiation of pre-emptive therapy for cytomegalovirus impacts overall survival in pediatric hematopoietic stem cell transplant recipients.
Cytotherapy
; 24(4): 428-436, 2022 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-35042670
18.
Viral infection in hematopoietic stem cell transplantation: an International Society for Cell & Gene Therapy Stem Cell Engineering Committee review on the role of cellular therapy in prevention and treatment.
Cytotherapy
; 24(9): 884-891, 2022 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-35705447
19.
Toxicity and response after CD19-specific CAR T-cell therapy in pediatric/young adult relapsed/refractory B-ALL.
Blood
; 134(26): 2361-2368, 2019 12 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-31650176
20.
Population pharmacokinetics of clofarabine for allogeneic hematopoietic cell transplantation in paediatric patients.
Br J Clin Pharmacol
; 87(8): 3218-3226, 2021 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-33444472