Detalhe da pesquisa
1.
Lumasiran, an RNAi Therapeutic for Primary Hyperoxaluria Type 1.
N Engl J Med
; 384(13): 1216-1226, 2021 04 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-33789010
2.
PHYOX2: a pivotal randomized study of nedosiran in primary hyperoxaluria type 1 or 2.
Kidney Int
; 103(1): 207-217, 2023 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36007597
3.
Clinical and molecular characterization of a large primary hyperoxaluria cohort from Saudi Arabia: a retrospective study.
Pediatr Nephrol
; 38(6): 1801-1810, 2023 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-36409364
4.
Safety, pharmacodynamics, and exposure-response modeling results from a first-in-human phase 1 study of nedosiran (PHYOX1) in primary hyperoxaluria.
Kidney Int
; 101(3): 626-634, 2022 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34481803
5.
Basket clinical trial design for targeted therapies for cancer: a French National Authority for Health statement for health technology assessment.
Lancet Oncol
; 22(10): e430-e434, 2021 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-34592192
6.
Interleukin 17 acts in synergy with B cell-activating factor to influence B cell biology and the pathophysiology of systemic lupus erythematosus.
Nat Immunol
; 10(7): 778-85, 2009 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-19483719
7.
Dynamic prediction models for graft failure in paediatric kidney transplantation.
Nephrol Dial Transplant
; 36(5): 927-935, 2021 04 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-32989448
8.
Comparison of iohexol plasma clearance formulas vs. inulin urinary clearance for measuring glomerular filtration rate.
Clin Chem Lab Med
; 59(3): 571-579, 2021 02 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-33068376
9.
Plasma oxalate and eGFR are correlated in primary hyperoxaluria patients with maintained kidney function-data from three placebo-controlled studies.
Pediatr Nephrol
; 36(7): 1785-1793, 2021 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-33515281
10.
Adherence to cysteamine in nephropathic cystinosis: A unique electronic monitoring experience for a better understanding. A prospective cohort study: CrYSTobs.
Pediatr Nephrol
; 36(3): 581-589, 2021 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-32901297
11.
Eplet incompatibility in pediatric renal transplantation.
Pediatr Transplant
; 24(6): e13721, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32388894
12.
Patients with primary hyperoxaluria type 2 have significant morbidity and require careful follow-up.
Kidney Int
; 96(6): 1389-1399, 2019 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-31685312
13.
Adverse events associated with currently used medical treatments for cystinuria and treatment goals: results from a series of 442 patients in France.
BJU Int
; 124(5): 849-861, 2019 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-30801923
14.
Towards adulthood with a solitary kidney.
Pediatr Nephrol
; 34(11): 2311-2323, 2019 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-30276534
15.
Skin microvascular dysfunction as an early cardiovascular marker in primary hyperoxaluria type I.
Pediatr Nephrol
; 34(2): 319-327, 2019 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-30276532
16.
Minoxidil versus placebo in the treatment of arterial wall hypertrophy in children with Williams Beuren Syndrome: a randomized controlled trial.
BMC Pediatr
; 19(1): 170, 2019 05 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-31138170
17.
Can requests for real-world evidence by the French HTA body be planned? An exhaustive retrospective case-control study of medicinal products appraisals from 2016 to 2021.
Int J Technol Assess Health Care
; : 1-25, 2024 May 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-38757153
18.
Bone disease in nephropathic cystinosis is related to cystinosin-induced osteoclastic dysfunction.
Nephrol Dial Transplant
; 33(9): 1525-1532, 2018 09 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-29365190
19.
Renal transplantation in children under 3 years of age: Experience from a single-center study.
Pediatr Transplant
; 22(2)2018 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-29341372
20.
IPNA-ESPN Junior Master Class-a decade of successful continuing education and training in pediatric nephrology.
Pediatr Nephrol
; 38(10): 3201-3205, 2023 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-37014529