Detalhe da pesquisa
1.
Exagamglogene Autotemcel for Transfusion-Dependent ß-Thalassemia.
N Engl J Med
; 390(18): 1663-1676, 2024 May 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-38657265
2.
Exagamglogene Autotemcel for Severe Sickle Cell Disease.
N Engl J Med
; 390(18): 1649-1662, 2024 May 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-38661449
3.
Busulfan-fludarabine- or treosulfan-fludarabine-based conditioning before allogeneic HSCT from matched sibling donors in paediatric patients with sickle cell disease: A study on behalf of the EBMT Paediatric Diseases and Inborn Errors Working Parties.
Br J Haematol
; 204(1): e1-e5, 2024 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-37795523
4.
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and ß-Thalassemia.
N Engl J Med
; 384(3): 252-260, 2021 01 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-33283989
5.
Matched unrelated donor transplantation versus haploidentical transplantation with post-transplant cyclophosphamide in children with acute myeloid leukemia: a PDWP-EBMT study.
Haematologica
; 2024 Jan 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-38186346
6.
Current challenges in cell and gene therapy: a joint view from the European Committee of the International Society for Cell & Gene Therapy (ISCT) and the European Society for Blood and Marrow Transplantation (EBMT).
Cytotherapy
; 2024 Feb 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-38416085
7.
Defining curative endpoints for sickle cell disease in the era of gene therapy and gene editing.
Am J Hematol
; 99(3): 430-438, 2024 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-38010293
8.
Defining curative endpoints for transfusion-dependent ß-thalassemia in the era of gene therapy and gene editing.
Am J Hematol
; 99(3): 422-429, 2024 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-38100154
9.
HLA-haploidentical stem cell transplantation in children with inherited bone marrow failure syndromes: A retrospective analysis on behalf of EBMT severe aplastic Anemia and pediatric diseases working parties.
Am J Hematol
; 99(6): 1066-1076, 2024 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-38497679
10.
Detection of a 7SL RNA-derived small non-coding RNA using Molecular Beacons in vitro and in cells.
Biol Chem
; 404(11-12): 1123-1136, 2023 10 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-37632732
11.
Feasibility of peripheral blood stem cell collection from sickle cell trait donors with an intensified G-CSF regimen.
Eur J Haematol
; 111(5): 824-830, 2023 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-37635081
12.
Haematopoietic stem cell transplantation for severe autoimmune diseases in children: A review of current literature, registry activity and future directions on behalf of the autoimmune diseases and paediatric diseases working parties of the European Society for Blood and Marrow Transplantation.
Br J Haematol
; 198(1): 24-45, 2022 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-37655707
13.
One and a half million hematopoietic stem cell transplants: continuous and differential improvement in worldwide access with the use of non-identical family donors.
Haematologica
; 107(5): 1045-1053, 2022 05 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-34382386
14.
Integrative medicine during the intensive phase of chemotherapy in pediatric oncology in Germany: a randomized controlled trial with 5-year follow up.
BMC Cancer
; 22(1): 652, 2022 Jun 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-35698215
15.
Granulocyte transfusions made with modified fluid gelatin in pediatric and adolescent patients with prolonged neutropenia.
Transfusion
; 62(2): 306-315, 2022 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-34910304
16.
Busulfan-fludarabine- or treosulfan-fludarabine-based myeloablative conditioning for children with thalassemia major.
Ann Hematol
; 101(3): 655-665, 2022 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-34999929
17.
Haplo-identical or mismatched unrelated donor hematopoietic cell transplantation for Fanconi anemia: Results from the Severe Aplastic Anemia Working Party of the EBMT.
Am J Hematol
; 96(5): 571-579, 2021 05 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-33606297
18.
Comparing mTOR inhibitor Rapamycin with Torin-2 within the RIST molecular-targeted regimen in neuroblastoma cells.
Int J Med Sci
; 18(1): 137-149, 2021.
Artigo
em Inglês
| MEDLINE | ID: mdl-33390782
19.
Incidence of Anicteric Veno-Occlusive Disease/Sinusoidal Obstruction Syndrome and Outcomes with Defibrotide following Hematopoietic Cell Transplantation in Adult and Pediatric Patients.
Biol Blood Marrow Transplant
; 26(7): 1342-1349, 2020 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-32200121
20.
Management of adults and children undergoing chimeric antigen receptor T-cell therapy: best practice recommendations of the European Society for Blood and Marrow Transplantation (EBMT) and the Joint Accreditation Committee of ISCT and EBMT (JACIE).
Haematologica
; 105(2): 297-316, 2020.
Artigo
em Inglês
| MEDLINE | ID: mdl-31753925