Detalhe da pesquisa
1.
In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model.
Gene Ther
; 30(5): 443-454, 2023 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-36450833
2.
Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice.
Gene Ther
; 28(10-11): 646-658, 2021 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-33558692
3.
Telomere dysfunction induces metabolic and mitochondrial compromise.
Nature
; 470(7334): 359-65, 2011 Feb 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-21307849
4.
Maintenance and repair of the lung endothelium does not involve contributions from marrow-derived endothelial precursor cells.
Am J Respir Cell Mol Biol
; 47(1): 11-9, 2012 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-22323363
5.
The in vivo genetic program of murine primordial lung epithelial progenitors.
Nat Commun
; 11(1): 635, 2020 01 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-32005814
6.
Endothelial protein C receptor (CD201) explicitly identifies hematopoietic stem cells in murine bone marrow.
Blood
; 107(6): 2317-21, 2006 Mar 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-16304059
7.
Complete correction of murine Artemis immunodeficiency by lentiviral vector-mediated gene transfer.
Proc Natl Acad Sci U S A
; 103(44): 16406-11, 2006 Oct 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-17062750
8.
A novel stem-cell population in adult liver with potent hematopoietic-reconstitution activity.
Blood
; 106(5): 1574-80, 2005 Sep 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-15870171
9.
Failure of bone marrow to reconstitute lung epithelium.
Am J Respir Cell Mol Biol
; 33(4): 328-34, 2005 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-15961722
10.
Efficiency of transduction of highly purified murine hematopoietic stem cells by lentiviral and oncoretroviral vectors under conditions of minimal in vitro manipulation.
Mol Ther
; 11(6): 932-40, 2005 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-15922964