Detalhe da pesquisa
1.
Adeno-Associated Virus Gene Therapy for Hemophilia.
Annu Rev Med
; 74: 231-247, 2023 01 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-36103998
2.
Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A.
N Engl J Med
; 385(21): 1961-1973, 2021 11 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-34788507
3.
Combining Surface-Induced Dissociation and Charge Detection Mass Spectrometry to Reveal the Native Topology of Heterogeneous Protein Complexes.
Anal Chem
; 95(37): 13889-13896, 2023 09 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-37672632
4.
Activated protein C has a regulatory role in factor VIII function.
Blood
; 137(18): 2532-2543, 2021 05 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-33512448
5.
Digital haemophilia: Insights into the use of social media for haemophilia care, research and advocacy.
Haemophilia
; 28(2): 247-253, 2022 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-35167716
6.
Appendix to the Society of Interventional Radiology Consensus Guidelines for the Periprocedural Management of Thrombotic and Bleeding Risk in Patients Undergoing Percutaneous Image-Guided Interventions: Pediatric Considerations.
J Vasc Interv Radiol
; 33(11): 1424-1431, 2022 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-35842024
7.
Mechanical ventilation variables associated with high pulmonary artery pressures in ARDS patients: a post hoc analysis.
Crit Care
; 26(1): 396, 2022 12 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-36544201
8.
Variable-Temperature Electrospray Ionization for Temperature-Dependent Folding/Refolding Reactions of Proteins and Ligand Binding.
Anal Chem
; 93(18): 6924-6931, 2021 05 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-33904705
9.
Gene Therapy for Inherited Bleeding Disorders.
Semin Thromb Hemost
; 47(2): 161-173, 2021 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-33636747
10.
Real-world cost estimates of initiating emicizumab in US patients with haemophilia A.
Haemophilia
; 27(4): 591-598, 2021 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-34050689
11.
Surface-induced dissociation of protein complexes on a cyclic ion mobility spectrometer.
Analyst
; 146(22): 6861-6873, 2021 Nov 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-34632987
12.
Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B.
Mol Ther
; 28(9): 2073-2082, 2020 09 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-32559433
13.
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
N Engl J Med
; 377(23): 2215-2227, 2017 12 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-29211678
14.
Collision Cross Sections of Charge-Reduced Proteins and Protein Complexes: A Database for Collision Cross Section Calibration.
Anal Chem
; 92(6): 4475-4483, 2020 03 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-32048834
15.
Immune tolerance induction by hepatic gene transfer: First-in-human evidence.
Mol Ther
; 32(4): 863-864, 2024 Apr 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-38518767
16.
Novel approaches to hemophilia therapy: successes and challenges.
Blood
; 130(21): 2251-2256, 2017 11 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-29018078
17.
MYH9-macrothrombocytopenia caused by a novel variant (E1421K) initially presenting as apparent neonatal alloimmune thrombocytopenia.
Pediatr Blood Cancer
; 65(4)2018 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-29286575
18.
Worldwide use of factor IX Padua for hemophilia B gene therapy.
Mol Ther
; 30(7): 2394-2396, 2022 07 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-35705095
19.
The influence of alcohol content variation in UK packaged beers on the uncertainty of calculations using the Widmark equation.
Sci Justice
; 58(4): 271-275, 2018 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-29895459
20.
Andexanet alfa for reversal of rivaroxaban in a child with intracranial hemorrhage.
Pediatr Blood Cancer
; 69(6): e29484, 2022 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-34811876