Detalhe da pesquisa
1.
Homology-Directed-Repair-Based Genome Editing in HSPCs for the Treatment of Inborn Errors of Immunity and Blood Disorders.
Pharmaceutics
; 15(5)2023 Apr 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-37242571
2.
CRISPR-Cas9 engineering of the RAG2 locus via complete coding sequence replacement for therapeutic applications.
Nat Commun
; 14(1): 6771, 2023 10 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-37891182
3.
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi.
Mol Ther Nucleic Acids
; 34: 102066, 2023 Dec 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-38034032