Detalhe da pesquisa
1.
Trial of Beremagene Geperpavec (B-VEC) for Dystrophic Epidermolysis Bullosa.
N Engl J Med
; 387(24): 2211-2219, 2022 12 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-36516090
2.
DIA's Adaptive Design Scientific Working Group (ADSWG): Best Practices Case Studies for "Less Well-understood" Adaptive Designs.
Ther Innov Regul Sci
; 51(1): 77-88, 2017 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-30235997
3.
Statistical challenges in drug approval trials that use patient-reported outcomes.
Stat Methods Med Res
; 23(5): 398-408, 2014 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-23435284
4.
Recommendations to Enhance Pediatric Cardiovascular Drug Development: Report of a Multi-Stakeholder Think Tank.
J Am Heart Assoc
; 7(4)2018 02 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-29440007
5.
Statistical considerations in the design, analysis and interpretation of clinical studies that use patient-reported outcomes.
Stat Methods Med Res
; 23(5): 393-7, 2014 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-25258383