Detalhe da pesquisa
1.
Hematopoietic stem cell collection for sickle cell disease gene therapy.
Curr Opin Hematol
; 31(3): 104-114, 2024 May 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-38359264
2.
Ex vivo culture resting time impacts transplantation outcomes of genome-edited human hematopoietic stem and progenitor cells in xenograft mouse models.
Cytotherapy
; 2024 Feb 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-38506770
3.
Genome editing strategies for fetal hemoglobin induction in beta-hemoglobinopathies.
Hum Mol Genet
; 29(R1): R100-R106, 2020 09 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-32406490
4.
Optimizing haematopoietic stem and progenitor cell apheresis collection from plerixafor-mobilized patients with sickle cell disease.
Br J Haematol
; 198(4): 740-744, 2022 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-35737751
5.
Curative therapy for hemoglobinopathies: an International Society for Cell & Gene Therapy Stem Cell Engineering Committee review comparing outcomes, accessibility and cost of ex vivo stem cell gene therapy versus allogeneic hematopoietic stem cell transplantation.
Cytotherapy
; 24(3): 249-261, 2022 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34879990
6.
Curative options for sickle cell disease: haploidentical stem cell transplantation or gene therapy?
Br J Haematol
; 189(3): 408-423, 2020 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-32034776
7.
A new frontier: FDA approvals for gene therapy in sickle cell disease.
Mol Ther
; 32(2): 264-267, 2024 Feb 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-38246166
8.
Bone marrow characterization in sickle cell disease: inflammation and stress erythropoiesis lead to suboptimal CD34 recovery.
Br J Haematol
; 186(2): 286-299, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30972754
9.
Identification of red blood cell antibodies in maternal breast milk implicated in prolonged hemolytic disease of the fetus and newborn.
Transfusion
; 59(4): 1183-1189, 2019 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-30720868
10.
CRISPR/Cas9 for Sickle Cell Disease: Applications, Future Possibilities, and Challenges.
Adv Exp Med Biol
; 1144: 37-52, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-30715679
11.
Early initiation of inhaled corticosteroids does not decrease acute chest syndrome morbidity in pediatric patients with sickle cell disease.
Blood Cells Mol Dis
; 71: 55-62, 2018 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-29550053
12.
A pause in gene therapy: Reflecting on the unique challenges of sickle cell disease.
Mol Ther
; 29(4): 1355-1356, 2021 04 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-33743192
13.
Safe and efficient peripheral blood stem cell collection in patients with sickle cell disease using plerixafor.
Haematologica
; 105(10): e497, 2020 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-33054091
14.
In vivo measurement of RBC survival in patients with sickle cell disease before or after hematopoietic stem cell transplantation.
Blood Adv
; 8(7): 1806-1816, 2024 Apr 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-38181784
15.
Gene therapy for sickle cell disease.
Hematology Am Soc Hematol Educ Program
; 2023(1): 542-547, 2023 Dec 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-38066927
16.
Outcomes and long-term effects of hematopoietic stem cell transplant in sickle cell disease.
Expert Rev Hematol
; 16(11): 879-903, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37800996
17.
Reduction in vaso-occlusive events following stem cell transplantation in patients with sickle cell disease.
Blood Adv
; 7(2): 227-234, 2023 01 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-36240296
18.
Clinical outcomes of children and adolescents with sickle cell disease and COVID-19 infection: A year in review at a metropolitan tertiary pediatric hospital.
Front Med (Lausanne)
; 10: 987194, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-36873869
19.
Forced enhancer-promoter rewiring to alter gene expression in animal models.
Mol Ther Nucleic Acids
; 31: 452-465, 2023 Mar 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-36852088
20.
Debating the Future of Sickle Cell Disease Curative Therapy: Haploidentical Hematopoietic Stem Cell Transplantation vs. Gene Therapy.
J Clin Med
; 11(16)2022 Aug 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-36013014