Detalhe da pesquisa
1.
Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access.
Lancet
; 399(10322): 372-383, 2022 01 22.
Artigo
em Inglês
| MEDLINE | ID: mdl-35065785
2.
Piezo1 controls cell volume and migration by modulating swelling-activated chloride current through Ca2+ influx.
J Cell Physiol
; 237(3): 1857-1870, 2022 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34913176
3.
The role of physical cues in the development of stem cell-derived organoids.
Eur Biophys J
; 51(2): 105-117, 2022 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-34120215
4.
De novo ssRNA Aptamers against the SARS-CoV-2 Main Protease: In Silico Design and Molecular Dynamics Simulation.
Int J Mol Sci
; 22(13)2021 Jun 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-34206794
5.
Interfacial Compatibilization into PLA/Mg Composites for Improved In Vitro Bioactivity and Stem Cell Adhesion.
Molecules
; 26(19)2021 Sep 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-34641488
6.
Novel bicistronic lentiviral vectors correct ß-Hexosaminidase deficiency in neural and hematopoietic stem cells and progeny: implications for in vivo and ex vivo gene therapy of GM2 gangliosidosis.
Neurobiol Dis
; 134: 104667, 2020 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-31682993
7.
Unpatterned Bioactive Poly(Butylene 1,4-Cyclohexanedicarboxylate)-Based Film Fast Induced Neuronal-Like Differentiation of Human Bone Marrow-Mesenchymal Stem Cells.
Int J Mol Sci
; 21(23)2020 Dec 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-33291757
8.
Insight into Mechanobiology: How Stem Cells Feel Mechanical Forces and Orchestrate Biological Functions.
Int J Mol Sci
; 20(21)2019 Oct 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-31717803
9.
Integrated Computational Analysis Highlights unique miRNA Signatures in the Subventricular Zone and Striatum of GM2 Gangliosidosis Animal Models.
Int J Mol Sci
; 20(13)2019 Jun 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-31261761
10.
Adipose Stem Cell Translational Applications: From Bench-to-Bedside.
Int J Mol Sci
; 19(11)2018 Nov 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-30400641
11.
Combined gene/cell therapies provide long-term and pervasive rescue of multiple pathological symptoms in a murine model of globoid cell leukodystrophy.
Hum Mol Genet
; 24(12): 3372-89, 2015 Jun 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-25749991
12.
Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial.
Lancet
; 388(10043): 476-87, 2016 Jul 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-27289174
13.
A Comparison of Lysosomal Enzymes Expression Levels in Peripheral Blood of Mild- and Severe-Alzheimer's Disease and MCI Patients: Implications for Regenerative Medicine Approaches.
Int J Mol Sci
; 18(8)2017 Aug 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-28825628
14.
Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy.
Hum Mol Genet
; 23(12): 3250-68, 2014 Jun 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-24463623
15.
A new analytical bench assay for the determination of arylsulfatase a activity toward galactosyl-3-sulfate ceramide: implication for metachromatic leukodystrophy diagnosis.
Anal Chem
; 86(1): 473-81, 2014 Jan 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-24294900
16.
Tight Regulation of Mechanotransducer Proteins Distinguishes the Response of Adult Multipotent Mesenchymal Cells on PBCE-Derivative Polymer Films with Different Hydrophilicity and Stiffness.
Cells
; 12(13)2023 06 29.
Artigo
em Inglês
| MEDLINE | ID: mdl-37443780
17.
Novel Nanostructured Scaffolds of Poly(butylene trans-1,4-cyclohexanedicarboxylate)-Based Copolymers with Tailored Hydrophilicity and Stiffness: Implication for Tissue Engineering Modeling.
Nanomaterials (Basel)
; 13(16)2023 Aug 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-37630915
18.
IL-3-zetakine combined with a CD33 costimulatory receptor as a dual CAR approach for safer and selective targeting of AML.
Blood Adv
; 7(12): 2855-2871, 2023 Jun 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-36521101
19.
Biochemical Pathways of Cellular Mechanosensing/Mechanotransduction and Their Role in Neurodegenerative Diseases Pathogenesis.
Cells
; 11(19)2022 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36231055
20.
Therapeutic advantages of combined gene/cell therapy strategies in a murine model of GM2 gangliosidosis.
Mol Ther Methods Clin Dev
; 25: 170-189, 2022 Jun 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-35434178