Detalhe da pesquisa
1.
Heterogeneity of reported outcomes in epidermolysis bullosa clinical research: a scoping review as a first step towards outcome harmonization.
Br J Dermatol
; 189(1): 80-90, 2023 07 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-37098154
2.
Mining scientific advice reports on cell-based products: Insight into the nonclinical development program.
Br J Clin Pharmacol
; 87(6): 2465-2474, 2021 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-32790909
3.
Therapeutic Prospects of Exon Skipping for Epidermolysis Bullosa.
Int J Mol Sci
; 22(22)2021 Nov 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-34830104
4.
Murine type VII collagen distorts outcome in human skin graft mouse model for dystrophic epidermolysis bullosa.
Exp Dermatol
; 28(10): 1153-1155, 2019 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30019435
5.
Harmonization of outcomes in epidermolysis bullosa: report of the Core Outcome Sets for Epidermolysis Bullosa (COSEB) kick-off meeting.
Br J Dermatol
; 190(2): 268-270, 2024 Jan 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-37792735
6.
Mutation in exon 1a of PLEC, leading to disruption of plectin isoform 1a, causes autosomal-recessive skin-only epidermolysis bullosa simplex.
Hum Mol Genet
; 24(11): 3155-62, 2015 Jun 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-25712130
7.
RNA-based therapies for genodermatoses.
Exp Dermatol
; 26(1): 3-10, 2017 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-27376675
8.
Pigmentation and melanocyte supply to the epidermis depend on type XVII collagen.
Exp Dermatol
; 23(2): 130-2, 2014 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-24330315
9.
Successful therapeutic transplantation of revertant skin in epidermolysis bullosa.
J Am Acad Dermatol
; 70(1): 98-101, 2014 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-24176523
10.
The Evolution of Drug Regulatory Sciences in the Netherlands: More than a Country Report.
Clin Pharmacol Ther
; 2024 Apr 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-38679943
11.
Translating Academic Drug Discovery Into Clinical Development: A Survey of the Awareness of Regulatory Support and Requirements Among Stakeholders in Europe.
Clin Pharmacol Ther
; 113(2): 349-359, 2023 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-36326573
12.
Access to medicines for rare diseases: A European regulatory roadmap for academia.
Front Pharmacol
; 14: 1142351, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-36925633
13.
Ethical challenges of using remote monitoring technologies for clinical research: A case study of the role of local research ethics committees in the RADAR-AD study.
PLoS One
; 18(7): e0285807, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37418385
14.
Correction: Ethical challenges of using remote monitoring technologies for clinical research: A case study of the role of local research ethics committees in the RADAR-AD study.
PLoS One
; 18(11): e0294797, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37972073
15.
Evaluation of Companion Diagnostics in Scientific Advice and Drug Marketing Authorization Applications by the European Medicines Agency.
Front Med (Lausanne)
; 9: 893028, 2022.
Artigo
em Inglês
| MEDLINE | ID: mdl-35602486
16.
Impact of the new European Union In Vitro Diagnostics Regulation on the practice of hospital diagnostic laboratories.
Expert Rev Mol Diagn
; 22(5): 583-590, 2022 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-35673983
17.
Revertant Mosaicism in Genodermatoses: Natural Gene Therapy Right before Your Eyes.
Biomedicines
; 10(9)2022 Aug 29.
Artigo
em Inglês
| MEDLINE | ID: mdl-36140224
18.
Medication Adherence Measurement Methods in Registration Trials Supporting the Approval of New Medicines: A Cross-Sectional Analysis of Centralized Procedures in the European Union 2010-2020.
Clin Pharmacol Ther
; 112(5): 1051-1060, 2022 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-35816103
19.
A Comparison of Post-marketing Measures Imposed by Regulatory Agencies to Confirm the Tissue-Agnostic Approach.
Front Med (Lausanne)
; 9: 893400, 2022.
Artigo
em Inglês
| MEDLINE | ID: mdl-35775007
20.
The Use of Remote Monitoring Technologies: A Review of Recent Regulatory Scientific Advices, Qualification Opinions, and Qualification Advices Issued by the European Medicines Agency.
Front Med (Lausanne)
; 8: 619513, 2021.
Artigo
em Inglês
| MEDLINE | ID: mdl-34277648