Detalhe da pesquisa
1.
An empowered, clinically viable hematopoietic stem cell gene therapy for the treatment of multisystemic mucopolysaccharidosis type II.
Mol Ther
; 32(3): 619-636, 2024 Mar 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-38310355
2.
The Role of Depression on Treatment Adherence in Patients with Heart Failure-a Systematic Review of the Literature.
Curr Cardiol Rep
; 24(12): 1995-2008, 2022 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-36327056
3.
Efficient Non-viral Gene Delivery into Human Hematopoietic Stem Cells by Minicircle Sleeping Beauty Transposon Vectors.
Mol Ther
; 26(4): 1137-1153, 2018 04 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-29503198
4.
Living beyond loss: a qualitative investigation of caregivers' experiences after the death of their relatives with amyotrophic lateral sclerosis.
Amyotroph Lateral Scler Frontotemporal Degener
; 25(1-2): 75-87, 2024 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-37674380
5.
Illness Perceptions, Cognitions, and Beliefs on COPD Patients' Adherence to Treatment - A Systematic Review.
Patient Prefer Adherence
; 17: 1845-1866, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37533752
6.
Prostaglandin E2 as transduction enhancer affects competitive engraftment of human hematopoietic stem and progenitor cells.
Mol Ther Methods Clin Dev
; 31: 101131, 2023 Dec 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-37920236
7.
An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model.
EMBO Mol Med
; 15(4): e15968, 2023 04 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-36876653
8.
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies.
Mol Ther Nucleic Acids
; 32: 229-246, 2023 Jun 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-37090420
9.
Designing Lentiviral Vectors for Gene Therapy of Genetic Diseases.
Viruses
; 13(8)2021 08 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-34452394
10.
Correction of laminin-5 deficiency in human epidermal stem cells by transcriptionally targeted lentiviral vectors.
Mol Ther
; 16(12): 1977-85, 2008 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-18813277
11.
Gene-Based Approaches to Inherited Neurometabolic Diseases.
Hum Gene Ther
; 30(10): 1222-1235, 2019 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-31397176
12.
Constraints on Human CD34+ Cell Fate due to Lentiviral Vectors Can Be Relieved by Valproic Acid.
Hum Gene Ther
; 30(8): 1023-1034, 2019 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-30977420
13.
Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCID.
Mol Ther Methods Clin Dev
; 15: 232-245, 2019 Dec 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-31720302
14.
Interactions between Retroviruses and the Host Cell Genome.
Mol Ther Methods Clin Dev
; 8: 31-41, 2018 Mar 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-29159201
15.
Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling ßAS3 Globin for Gene Therapy for Sickle Cell Disease.
Mol Ther Methods Clin Dev
; 11: 167-179, 2018 Dec 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-30533448
16.
Gene Therapy for Sickle Cell Disease: A Lentiviral Vector Comparison Study.
Hum Gene Ther
; 29(10): 1153-1166, 2018 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30198339
17.
Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency.
Mol Ther Methods Clin Dev
; 9: 257-269, 2018 Jun 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-29707600
18.
Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for ß-Thalassemia.
Mol Ther Methods Clin Dev
; 11: 9-28, 2018 Dec 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-30320151
19.
An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype.
Mol Ther Methods Clin Dev
; 10: 268-280, 2018 Sep 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-30140714
20.
Retroviral Scanning: Mapping MLV Integration Sites to Define Cell-specific Regulatory Regions.
J Vis Exp
; (123)2017 05 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-28605390