Detalhe da pesquisa
1.
Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease.
N Engl J Med
; 386(7): 617-628, 2022 02 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-34898139
2.
An integrated therapeutic approach to sickle cell disease management beyond infancy.
Am J Hematol
; 98(7): 1087-1096, 2023 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-37170801
3.
Lovo-cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB-206 study.
Am J Hematol
; 98(1): 11-22, 2023 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36161320
4.
Pregnancy outcome in women with transfused beta-thalassemia in France.
Ann Hematol
; 101(2): 289-296, 2022 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-34668980
5.
Gene Therapy in Patients with Transfusion-Dependent ß-Thalassemia.
N Engl J Med
; 378(16): 1479-1493, 2018 04 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-29669226
6.
Gene Therapy in a Patient with Sickle Cell Disease.
N Engl J Med
; 376(9): 848-855, 2017 03 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-28249145
7.
A novel, highly potent and selective phosphodiesterase-9 inhibitor for the treatment of sickle cell disease.
Haematologica
; 105(3): 623-631, 2020 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-31147439
8.
HSP70 sequestration by free α-globin promotes ineffective erythropoiesis in ß-thalassaemia.
Nature
; 514(7521): 242-6, 2014 Oct 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-25156257
9.
Sotatercept, a novel transforming growth factor ß ligand trap, improves anemia in ß-thalassemia: a phase II, open-label, dose-finding study.
Haematologica
; 104(3): 477-484, 2019 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-30337358
10.
Plerixafor enables safe, rapid, efficient mobilization of hematopoietic stem cells in sickle cell disease patients after exchange transfusion.
Haematologica
; 103(5): 778-786, 2018 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-29472357
11.
Transfusion-related adverse events are decreased in pregnant women with sickle cell disease by a change in policy from systematic transfusion to prophylactic oxygen therapy at home: A retrospective survey by the international sickle cell disease observatory.
Am J Hematol
; 93(6): 794-802, 2018 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-29603363
12.
Roles of APOL1 G1 and G2 variants in sickle cell disease patients: kidney is the main target.
Br J Haematol
; 179(2): 323-335, 2017 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-28699644
13.
Primary myelofibrosis in untreated sickle cell disease: Are adult patients at higher risk for developing hematological myeloid neoplasms?
Am J Hematol
; 97(1): 4-6, 2022 01 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-34626435
14.
Arterio-venous fistula for automated red blood cells exchange in patients with sickle cell disease: Complications and outcomes.
Am J Hematol
; 92(2): 136-140, 2017 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-27813144
15.
Safety and feasibility of hematopoietic progenitor stem cell collection by mobilization with plerixafor followed by apheresis vs bone marrow harvest in patients with sickle cell disease in the multi-center HGB-206 trial.
Am J Hematol
; 95(9): E239-E242, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32401372
16.
A biomimetic microfluidic chip to study the circulation and mechanical retention of red blood cells in the spleen.
Am J Hematol
; 90(4): 339-45, 2015 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-25641515
17.
Defective nuclear localization of Hsp70 is associated with dyserythropoiesis and GATA-1 cleavage in myelodysplastic syndromes.
Blood
; 119(6): 1532-42, 2012 Feb 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-22160620
18.
A specific time course for mobilization of peripheral blood CD34+ cells after plerixafor injection in very poor mobilizer patients: impact on the timing of the apheresis procedure.
Transfusion
; 53(3): 564-9, 2013 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-22725259
19.
Hsp70 regulates erythropoiesis by preventing caspase-3-mediated cleavage of GATA-1.
Nature
; 445(7123): 102-5, 2007 Jan 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-17167422
20.
Ineffective erythropoiesis in ß -thalassemia.
ScientificWorldJournal
; 2013: 394295, 2013.
Artigo
em Inglês
| MEDLINE | ID: mdl-23606813