Detalhe da pesquisa
1.
A macaque clonal hematopoiesis model demonstrates expansion of TET2-disrupted clones and utility for testing interventions.
Blood
; 140(16): 1774-1789, 2022 10 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-35714307
2.
Ex vivo culture resting time impacts transplantation outcomes of genome-edited human hematopoietic stem and progenitor cells in xenograft mouse models.
Cytotherapy
; 2024 Feb 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-38506770
3.
Large-scale purification of functional AAV particles packaging the full genome using short-term ultracentrifugation with a zonal rotor.
Gene Ther
; 30(7-8): 641-648, 2023 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-36977769
4.
Lovo-cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB-206 study.
Am J Hematol
; 98(1): 11-22, 2023 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36161320
5.
Evaluation of genetic diversity using 31 microsatellites in Miyako horses.
J Equine Sci
; 34(1): 1-6, 2023 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-37155490
6.
Optimizing haematopoietic stem and progenitor cell apheresis collection from plerixafor-mobilized patients with sickle cell disease.
Br J Haematol
; 198(4): 740-744, 2022 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-35737751
7.
Busulfan Combined with Immunosuppression Allows Efficient Engraftment of Gene-Modified Cells in a Rhesus Macaque Model.
Mol Ther
; 27(9): 1586-1596, 2019 09 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-31253582
8.
Aberrant Clonal Hematopoiesis following Lentiviral Vector Transduction of HSPCs in a Rhesus Macaque.
Mol Ther
; 27(6): 1074-1086, 2019 06 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-31023523
9.
Bone marrow characterization in sickle cell disease: inflammation and stress erythropoiesis lead to suboptimal CD34 recovery.
Br J Haematol
; 186(2): 286-299, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30972754
10.
Ex vivo immunological evaluation of stable mixed chimeric patients after matched related donor allogeneic transplantation in sickle cell disease.
Cytotherapy
; 21(12): 1206-1215, 2019 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-31784240
11.
CRISPR/Cas9 for Sickle Cell Disease: Applications, Future Possibilities, and Challenges.
Adv Exp Med Biol
; 1144: 37-52, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-30715679
12.
Efficient Generation of ß-Globin-Expressing Erythroid Cells Using Stromal Cell-Derived Induced Pluripotent Stem Cells from Patients with Sickle Cell Disease.
Stem Cells
; 35(3): 586-596, 2017 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-27739611
13.
Gene therapy for sickle cell disease: An update.
Cytotherapy
; 20(7): 899-910, 2018 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-29859773
14.
Robust erythroid differentiation system for rhesus hematopoietic progenitor cells allowing preclinical screening of genetic treatment strategies for the hemoglobinopathies.
Cytotherapy
; 20(10): 1278-1287, 2018 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30249524
15.
Discordance in lymphoid tissue recovery following stem cell transplantation in rhesus macaques: an in vivo imaging study.
Blood
; 126(24): 2632-41, 2015 Dec 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-26492933
16.
ß-Globin-Expressing Definitive Erythroid Progenitor Cells Generated from Embryonic and Induced Pluripotent Stem Cell-Derived Sacs.
Stem Cells
; 34(6): 1541-52, 2016 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-26866725
17.
Comparison of CD34+ cells isolated from frozen cord blood and fresh adult peripheral blood of sickle cell disease patients in gene correction of the sickle mutation at late-stage erythroid differentiation.
Br J Haematol
; 194(5): e80-e84, 2021 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-34060073
18.
Commentary on Winzeler et al 'Low arginine vasopressin levels in patients with diabetes insipidus are not associated with anaemia'.
Clin Endocrinol (Oxf)
; 94(5): 888-890, 2021 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-33314284
19.
MASL1 induces erythroid differentiation in human erythropoietin-dependent CD34+ cells through the Raf/MEK/ERK pathway.
Blood
; 121(16): 3216-27, 2013 Apr 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-23327923
20.
Safe and efficient peripheral blood stem cell collection in patients with sickle cell disease using plerixafor.
Haematologica
; 105(10): e497, 2020 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-33054091