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The human ankyrin 1 promoter insulator sustains gene expression in a ß-globin lentiviral vector in hematopoietic stem cells.
Romero, Zulema; Campo-Fernandez, Beatriz; Wherley, Jennifer; Kaufman, Michael L; Urbinati, Fabrizia; Cooper, Aaron R; Hoban, Megan D; Baldwin, Kismet M; Lumaquin, Dianne; Wang, Xiaoyan; Senadheera, Shantha; Hollis, Roger P; Kohn, Donald B.
Afiliação
  • Romero Z; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Campo-Fernandez B; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Wherley J; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Kaufman ML; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Urbinati F; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Cooper AR; Molecular Biology Interdepartmental PhD Program, University of California , Los Angeles, California, USA.
  • Hoban MD; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Baldwin KM; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Lumaquin D; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Wang X; Department of Internal Medicine and Health Services Research, University of California , Los Angeles, California, USA.
  • Senadheera S; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Hollis RP; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA.
  • Kohn DB; Department of Microbiology, Immunology and Molecular Genetics, University of California , Los Angeles, California, USA ; Department of Pediatrics, UCLA Children's Discovery and Innovation Institute David Geffen School of Medicine, University of California , Los Angeles, California, USA.
Mol Ther Methods Clin Dev ; 2: 15012, 2015.
Article em En | MEDLINE | ID: mdl-26029723

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Ano de publicação: 2015 Tipo de documento: Article