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Gender-Specific Amelioration of SMA Phenotype upon Disruption of a Deep Intronic Structure by an Oligonucleotide.
Howell, Matthew D; Ottesen, Eric W; Singh, Natalia N; Anderson, Rachel L; Singh, Ravindra N.
Afiliação
  • Howell MD; Department of Biomedical Sciences, Iowa State University, Ames, IA 50011, USA.
  • Ottesen EW; Department of Biomedical Sciences, Iowa State University, Ames, IA 50011, USA.
  • Singh NN; Department of Biomedical Sciences, Iowa State University, Ames, IA 50011, USA.
  • Anderson RL; Department of Biomedical Sciences, Iowa State University, Ames, IA 50011, USA.
  • Singh RN; Department of Biomedical Sciences, Iowa State University, Ames, IA 50011, USA. Electronic address: singhr@iastate.edu.
Mol Ther ; 25(6): 1328-1341, 2017 06 07.
Article em En | MEDLINE | ID: mdl-28412171

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Animals Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Animals Idioma: En Ano de publicação: 2017 Tipo de documento: Article