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Improved molecular platform for the gene therapy of rare diseases by liver protein secretion.
Quiviger, Mickael; Giannakopoulos, Aristeidis; Verhenne, Sebastien; Marie, Corinne; Stavrou, Eleana F; Vanhoorelbeke, Karen; Izsvák, Zsuzsanna; De Meyer, Simon F; Athanassiadou, Aglaia; Scherman, Daniel.
Afiliação
  • Quiviger M; Laboratory of Chemical and Biological Technologies for Health, Université Paris Descartes, Sorbonne-Paris-Cité, F-75006 Paris, France; CNRS, UTCBS UMR 8258, F-75006 Paris, France; Chimie ParisTech, PSL Research University, UTCBS, F-75005 Paris, France; INSERM, UTCBS U 1022, F-75006 Paris, France.
  • Giannakopoulos A; Department of General Biology, Medical School, University of Patras, Rion, Greece.
  • Verhenne S; Laboratory for Thrombosis Research, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium.
  • Marie C; Laboratory of Chemical and Biological Technologies for Health, Université Paris Descartes, Sorbonne-Paris-Cité, F-75006 Paris, France; CNRS, UTCBS UMR 8258, F-75006 Paris, France; Chimie ParisTech, PSL Research University, UTCBS, F-75005 Paris, France; INSERM, UTCBS U 1022, F-75006 Paris, France.
  • Stavrou EF; Department of General Biology, Medical School, University of Patras, Rion, Greece.
  • Vanhoorelbeke K; Laboratory for Thrombosis Research, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium.
  • Izsvák Z; Mobile DNA, Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), Berlin, Germany.
  • De Meyer SF; Laboratory for Thrombosis Research, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium.
  • Athanassiadou A; Department of General Biology, Medical School, University of Patras, Rion, Greece.
  • Scherman D; Laboratory of Chemical and Biological Technologies for Health, Université Paris Descartes, Sorbonne-Paris-Cité, F-75006 Paris, France; CNRS, UTCBS UMR 8258, F-75006 Paris, France; Chimie ParisTech, PSL Research University, UTCBS, F-75005 Paris, France; INSERM, UTCBS U 1022, F-75006 Paris, France. El
Eur J Med Genet ; 61(11): 723-728, 2018 Nov.
Article em En | MEDLINE | ID: mdl-29704684

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Limite: Humans Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Limite: Humans Idioma: En Ano de publicação: 2018 Tipo de documento: Article