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Adenine Base Editing In Vivo with a Single Adeno-Associated Virus Vector.
Zhang, Han; Bamidele, Nathan; Liu, Pengpeng; Ojelabi, Ogooluwa; Gao, Xin D; Rodriguez, Tomás; Cheng, Haoyang; Kelly, Karen; Watts, Jonathan K; Xie, Jun; Gao, Guangping; Wolfe, Scot A; Xue, Wen; Sontheimer, Erik J.
Afiliação
  • Zhang H; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Bamidele N; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Liu P; Departments of Molecular, Cell and Cancer Biology, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Ojelabi O; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Gao XD; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Rodriguez T; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Cheng H; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Kelly K; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Watts JK; RNA Therapeutics Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Xie J; Departments of Biochemistry and Molecular Biotechnology, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Gao G; NeuroNexus Institute, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Wolfe SA; Horae Gene Therapy Center, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Xue W; Viral Vector Core, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
  • Sontheimer EJ; Departments of Microbiology and Physiological Systems, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA..
GEN Biotechnol ; 1(3): 285-299, 2022 Jun 01.
Article em En | MEDLINE | ID: mdl-35811581

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Risk_factors_studies Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Risk_factors_studies Idioma: En Ano de publicação: 2022 Tipo de documento: Article