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Long-term nusinersen treatment across a wide spectrum of spinal muscular atrophy severity: a real-world experience.
Lusakowska, Anna; Wójcik, Adrianna; Fraczek, Anna; Aragon-Gawinska, Karolina; Potulska-Chromik, Anna; Baranowski, Pawel; Nowak, Ryszard; Rosiak, Grzegorz; Milczarek, Krzysztof; Konecki, Dariusz; Gierlak-Wójcicka, Zuzanna; Burlewicz, Malgorzata; Kostera-Pruszczyk, Anna.
Afiliação
  • Lusakowska A; Department of Neurology, Medical University of Warsaw, ERN EURO-NMD, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Wójcik A; Department of Neurology and Stroke, Ludwik Rydygier Specialist Hospital, Osiedle Zlotej Jesieni 1, Kraków, 31-826, Poland.
  • Fraczek A; Department of Neurology, Medical University of Warsaw, ERN EURO-NMD, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Aragon-Gawinska K; Department of Neurology, Medical University of Warsaw, ERN EURO-NMD, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Potulska-Chromik A; Department of Neurology, Medical University of Warsaw, ERN EURO-NMD, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Baranowski P; Department of Econometrics, Faculty of Economics and Sociology, University of Lódz, ul. Rewolucji 1905 37/39, Lódz, 90-214, Poland.
  • Nowak R; Department of Neurology and Stroke, Ludwik Rydygier Specialist Hospital, Osiedle Zlotej Jesieni 1, Kraków, 31-826, Poland.
  • Rosiak G; Department of Radiology, Medical University of Warsaw, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Milczarek K; Department of Radiology, Medical University of Warsaw, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Konecki D; Department of Radiology, Medical University of Warsaw, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Gierlak-Wójcicka Z; Department of Neurology, Medical University of Warsaw, ERN EURO-NMD, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Burlewicz M; Department of Neurology, Medical University of Warsaw, ERN EURO-NMD, ul. Banacha 1a, Warsaw, 02-097, Poland.
  • Kostera-Pruszczyk A; Department of Neurology, Medical University of Warsaw, ERN EURO-NMD, ul. Banacha 1a, Warsaw, 02-097, Poland. anna.kostera-pruszczyk@wum.edu.pl.
Orphanet J Rare Dis ; 18(1): 230, 2023 08 04.
Article em En | MEDLINE | ID: mdl-37542300

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Limite: Adolescent / Adult / Child / Humans / Infant Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Limite: Adolescent / Adult / Child / Humans / Infant Idioma: En Ano de publicação: 2023 Tipo de documento: Article