Detalhe da pesquisa
1.
Lentiviral vector ALS20 yields high hemoglobin levels with low genomic integrations for treatment of beta-globinopathies.
Mol Ther
; 29(4): 1625-1638, 2021 04 07.
Artigo
Inglês
| MEDLINE | ID: mdl-33515514
2.
Metastatic Mixed Germ Cell Tumour with Embryonal Carcinoma and Choriocarcinoma in a Female Eurasian Harvest Mouse (Micromys minutus).
J Comp Pathol
; 180: 122-127, 2020 Oct.
Artigo
Inglês
| MEDLINE | ID: mdl-33222869
3.
Krabbe disease successfully treated via monotherapy of intrathecal gene therapy.
J Clin Invest
; 130(9): 4906-4920, 2020 09 01.
Artigo
Inglês
| MEDLINE | ID: mdl-32773406