Detalhe da pesquisa
1.
Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy.
Mol Ther
; 29(1): 86-102, 2021 01 06.
Artigo
Inglês
| MEDLINE | ID: mdl-33010230
2.
Alterations in the adenosine metabolism and CD39/CD73 adenosinergic machinery cause loss of Treg cell function and autoimmunity in ADA-deficient SCID.
Blood
; 119(6): 1428-39, 2012 Feb 09.
Artigo
Inglês
| MEDLINE | ID: mdl-22184407
3.
mRNA COVID-19 vaccine booster fosters B- and T-cell responses in immunocompromised patients.
Life Sci Alliance
; 5(6)2022 06.
Artigo
Inglês
| MEDLINE | ID: mdl-35169017
4.
Conditioning Regimens in Long-Term Pre-Clinical Studies to Support Development of Ex Vivo Gene Therapy: Review of Nonproliferative and Proliferative Changes.
Hum Gene Ther
; 32(1-2): 66-76, 2021 01.
Artigo
Inglês
| MEDLINE | ID: mdl-32883113
5.
Good Laboratory Practice Preclinical Safety Studies for GSK2696273 (MLV Vector-Based Ex Vivo Gene Therapy for Adenosine Deaminase Deficiency Severe Combined Immunodeficiency) in NSG Mice.
Hum Gene Ther Clin Dev
; 28(1): 17-27, 2017 03.
Artigo
Inglês
| MEDLINE | ID: mdl-28319446
6.
Alterations in the brain adenosine metabolism cause behavioral and neurological impairment in ADA-deficient mice and patients.
Sci Rep
; 7: 40136, 2017 01 11.
Artigo
Inglês
| MEDLINE | ID: mdl-28074903
7.
Progress in gene therapy for primary immunodeficiencies using lentiviral vectors.
Curr Opin Allergy Clin Immunol
; 14(6): 527-34, 2014 Dec.
Artigo
Inglês
| MEDLINE | ID: mdl-25207699
8.
Autoimmune dysregulation and purine metabolism in adenosine deaminase deficiency.
Front Immunol
; 3: 265, 2012.
Artigo
Inglês
| MEDLINE | ID: mdl-22969765