Detalhe da pesquisa
1.
Lentiviral Gene Therapy for Artemis-Deficient SCID.
N Engl J Med
; 387(25): 2344-2355, 2022 12 22.
Artigo
Inglês
| MEDLINE | ID: mdl-36546626
2.
Genotype, oxidase status, and preceding infection or autoinflammation do not affect allogeneic HCT outcomes for CGD.
Blood
; 142(24): 2105-2118, 2023 12 14.
Artigo
Inglês
| MEDLINE | ID: mdl-37562003
3.
Posttransplantation late complications increase over time for patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) landmark study.
J Allergy Clin Immunol
; 153(1): 287-296, 2024 01.
Artigo
Inglês
| MEDLINE | ID: mdl-37793572
4.
Allogeneic hematopoietic cell transplantation is effective for p47phox chronic granulomatous disease: A Primary Immune Deficiency Treatment Consortium study.
J Allergy Clin Immunol
; 153(5): 1423-1431.e2, 2024 May.
Artigo
Inglês
| MEDLINE | ID: mdl-38290608
5.
Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium.
Lancet
; 402(10396): 129-140, 2023 07 08.
Artigo
Inglês
| MEDLINE | ID: mdl-37352885
6.
Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC.
Blood
; 140(7): 685-705, 2022 08 18.
Artigo
Inglês
| MEDLINE | ID: mdl-35671392
7.
The role of donor type and pre-transplant immunosuppression on outcomes of hematopoietic stem cell transplantation in children and young adults with severe aplastic anemia.
Pediatr Transplant
; 28(4): e14784, 2024 Jun.
Artigo
Inglês
| MEDLINE | ID: mdl-38766976
8.
The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions.
J Allergy Clin Immunol
; 151(2): 547-555.e5, 2023 02.
Artigo
Inglês
| MEDLINE | ID: mdl-36456360
9.
Intestinal microbiome and metabolome signatures in patients with chronic granulomatous disease.
J Allergy Clin Immunol
; 152(6): 1619-1633.e11, 2023 12.
Artigo
Inglês
| MEDLINE | ID: mdl-37659505
10.
Comparison of hematopoietic cell transplant conditioning regimens for hemophagocytic lymphohistiocytosis disorders.
J Allergy Clin Immunol
; 149(3): 1097-1104.e2, 2022 03.
Artigo
Inglês
| MEDLINE | ID: mdl-34375618
11.
Granulocyte Transfusions in Patients with Chronic Granulomatous Disease Undergoing Hematopoietic Cell Transplantation or Gene Therapy.
J Clin Immunol
; 42(5): 1026-1035, 2022 07.
Artigo
Inglês
| MEDLINE | ID: mdl-35445907
12.
Excellent outcomes following hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report.
Blood
; 135(23): 2094-2105, 2020 06 04.
Artigo
Inglês
| MEDLINE | ID: mdl-32268350
13.
Race as a factor in donor selection and survival of children with hematologic malignancies undergoing hematopoietic stem cell transplant in Florida.
Pediatr Blood Cancer
; 68(10): e29180, 2021 10.
Artigo
Inglês
| MEDLINE | ID: mdl-34121322
14.
Pediatric HCT in Florida (2014 -2016): A report from the FPBCC.
Pediatr Transplant
; 25(5): e13931, 2021 08.
Artigo
Inglês
| MEDLINE | ID: mdl-33245834
15.
Correction: Chronic Granulomatous Disease-Associated IBD Resolves and Does Not Adversely Impact Survival Following Allogeneic HCT.
J Clin Immunol
; 40(8): 1211-1213, 2020 Nov.
Artigo
Inglês
| MEDLINE | ID: mdl-32860171
16.
Haploidentical bone marrow transplantation in a patient with sickle cell disease and acute myeloid leukemia.
Pediatr Transplant
; 24(1): e13641, 2020 02.
Artigo
Inglês
| MEDLINE | ID: mdl-31880407
17.
A multicenter study of patients with multisystem Langerhans cell histiocytosis who develop secondary hemophagocytic lymphohistiocytosis.
Cancer
; 125(6): 963-971, 2019 03 15.
Artigo
Inglês
| MEDLINE | ID: mdl-30521100
18.
Chronic Granulomatous Disease-Associated IBD Resolves and Does Not Adversely Impact Survival Following Allogeneic HCT.
J Clin Immunol
; 39(7): 653-667, 2019 10.
Artigo
Inglês
| MEDLINE | ID: mdl-31376032
19.
Successful Allogeneic Hematopoietic Stem Cell Transplantation in XIAP Deficiency Using Reduced-Intensity Conditioning.
Pediatr Blood Cancer
; 63(2): 355-7, 2016 Feb.
Artigo
Inglês
| MEDLINE | ID: mdl-26398727
20.
Management and Outcome of Patients With Langerhans Cell Histiocytosis and Single-Bone CNS-Risk Lesions: A Multi-Institutional Retrospective Study.
Pediatr Blood Cancer
; 62(12): 2162-6, 2015 Dec.
Artigo
Inglês
| MEDLINE | ID: mdl-26179251