Detalhe da pesquisa
1.
Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patients.
Blood
; 129(19): 2624-2635, 2017 05 11.
Artigo
Inglês
| MEDLINE | ID: mdl-28351939
2.
Characterization of Gene Alterations following Editing of the ß-Globin Gene Locus in Hematopoietic Stem/Progenitor Cells.
Mol Ther
; 26(2): 468-479, 2018 02 07.
Artigo
Inglês
| MEDLINE | ID: mdl-29221806
3.
Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells.
Blood
; 125(17): 2597-604, 2015 Apr 23.
Artigo
Inglês
| MEDLINE | ID: mdl-25733580
4.
Genetic Tagging During Human Mesoderm Differentiation Reveals Tripotent Lateral Plate Mesodermal Progenitors.
Stem Cells
; 34(5): 1239-50, 2016 05.
Artigo
Inglês
| MEDLINE | ID: mdl-26934332
5.
CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells.
Mol Ther
; 24(9): 1561-9, 2016 09.
Artigo
Inglês
| MEDLINE | ID: mdl-27406980
6.
Rescue of splicing-mediated intron loss maximizes expression in lentiviral vectors containing the human ubiquitin C promoter.
Nucleic Acids Res
; 43(1): 682-90, 2015 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-25520191
7.
Enrichment of human hematopoietic stem/progenitor cells facilitates transduction for stem cell gene therapy.
Stem Cells
; 33(5): 1532-42, 2015 May.
Artigo
Inglês
| MEDLINE | ID: mdl-25588820
8.
Long-term in vivo monitoring of mouse and human hematopoietic stem cell engraftment with a human positron emission tomography reporter gene.
Proc Natl Acad Sci U S A
; 110(5): 1857-62, 2013 Jan 29.
Artigo
Inglês
| MEDLINE | ID: mdl-23319634
9.
Prostate cancer originating in basal cells progresses to adenocarcinoma propagated by luminal-like cells.
Proc Natl Acad Sci U S A
; 110(50): 20111-6, 2013 Dec 10.
Artigo
Inglês
| MEDLINE | ID: mdl-24282295
10.
Swab-Seq: A high-throughput platform for massively scaled up SARS-CoV-2 testing.
medRxiv
; 2021 Mar 09.
Artigo
Inglês
| MEDLINE | ID: mdl-32909008
11.
Massively scaled-up testing for SARS-CoV-2 RNA via next-generation sequencing of pooled and barcoded nasal and saliva samples.
Nat Biomed Eng
; 5(7): 657-665, 2021 07.
Artigo
Inglês
| MEDLINE | ID: mdl-34211145
12.
Reliable and accurate diagnostics from highly multiplexed sequencing assays.
Sci Rep
; 10(1): 21759, 2020 12 10.
Artigo
Inglês
| MEDLINE | ID: mdl-33303831
13.
Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome.
Cell Rep
; 23(9): 2606-2616, 2018 05 29.
Artigo
Inglês
| MEDLINE | ID: mdl-29847792
14.
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.
J Clin Invest
; 127(5): 1689-1699, 2017 May 01.
Artigo
Inglês
| MEDLINE | ID: mdl-28346229
15.
The human ankyrin 1 promoter insulator sustains gene expression in a ß-globin lentiviral vector in hematopoietic stem cells.
Mol Ther Methods Clin Dev
; 2: 15012, 2015.
Artigo
Inglês
| MEDLINE | ID: mdl-26029723
16.
ß-globin gene transfer to human bone marrow for sickle cell disease.
J Clin Invest
; 2013 Jul 01.
Artigo
Inglês
| MEDLINE | ID: mdl-23863630
17.
From skin biopsy to neurons through a pluripotent intermediate under Good Manufacturing Practice protocols.
Stem Cells Transl Med
; 1(1): 36-43, 2012 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-23197638
18.
Highly efficient large-scale lentiviral vector concentration by tandem tangential flow filtration.
J Virol Methods
; 177(1): 1-9, 2011 Oct.
Artigo
Inglês
| MEDLINE | ID: mdl-21784103