Detalhe da pesquisa
1.
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
N Engl J Med
; 384(21): 2002-2013, 2021 05 27.
Artigo
Inglês
| MEDLINE | ID: mdl-33974366
2.
Implementation of a gene therapy education initiative by the ASGCT and Muhimbili University of Health and Allied Sciences.
Mol Ther
; 31(9): 2561-2565, 2023 09 06.
Artigo
Inglês
| MEDLINE | ID: mdl-37595584
3.
Replication competent retrovirus testing (RCR) in the National Gene Vector Biorepository: No evidence of RCR in 1,595 post-treatment peripheral blood samples obtained from 60 clinical trials.
Mol Ther
; 31(3): 801-809, 2023 03 01.
Artigo
Inglês
| MEDLINE | ID: mdl-36518078
4.
Impact of training on knowledge, confidence and attitude amongst community health volunteers in the provision of community-based palliative care in rural Kenya.
BMC Palliat Care
; 23(1): 97, 2024 Apr 11.
Artigo
Inglês
| MEDLINE | ID: mdl-38605309
5.
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency.
Blood
; 138(15): 1304-1316, 2021 10 14.
Artigo
Inglês
| MEDLINE | ID: mdl-33974038
6.
Gene therapy access: Global challenges, opportunities, and views from Brazil, South Africa, and India.
Mol Ther
; 30(6): 2122-2129, 2022 06 01.
Artigo
Inglês
| MEDLINE | ID: mdl-35390542
7.
Transitioning from development to commercial: risk-based guidance for critical materials management in cell therapies.
Cytotherapy
; 22(11): 669-676, 2020 11.
Artigo
Inglês
| MEDLINE | ID: mdl-32713719
8.
Absence of Replication-Competent Lentivirus in the Clinic: Analysis of Infused T Cell Products.
Mol Ther
; 26(1): 280-288, 2018 01 03.
Artigo
Inglês
| MEDLINE | ID: mdl-28970045
9.
AAV Joins the Rank of Genotoxic Vectors.
Mol Ther
; 29(2): 418-419, 2021 02 03.
Artigo
Inglês
| MEDLINE | ID: mdl-33472035
10.
Transfusion independence and HMGA2 activation after gene therapy of human ß-thalassaemia.
Nature
; 467(7313): 318-22, 2010 Sep 16.
Artigo
Inglês
| MEDLINE | ID: mdl-20844535
11.
[(18)F]FHBG PET/CT Imaging of CD34-TK75 Transduced Donor T Cells in Relapsed Allogeneic Stem Cell Transplant Patients: Safety and Feasibility.
Mol Ther
; 23(6): 1110-1122, 2015 Jun.
Artigo
Inglês
| MEDLINE | ID: mdl-25807290
12.
Gene Transfer to HSCs: Finding the Leukemia in Murine Leukemia Viruses.
Mol Ther
; 27(6): 1072-1073, 2019 06 05.
Artigo
Inglês
| MEDLINE | ID: mdl-31109833
13.
Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency.
Mol Ther
; 22(3): 607-622, 2014 Mar.
Artigo
Inglês
| MEDLINE | ID: mdl-24256635
14.
Equitable Access to Gene Therapy: A Call to Action for the American Society of Gene and Cell Therapy.
Mol Ther
; 26(12): 2715-2716, 2018 12 05.
Artigo
Inglês
| MEDLINE | ID: mdl-30454956
15.
Platelet gene therapy improves hemostatic function for integrin alphaIIbbeta3-deficient dogs.
Proc Natl Acad Sci U S A
; 108(23): 9583-8, 2011 Jun 07.
Artigo
Inglês
| MEDLINE | ID: mdl-21606353
16.
The translational gap for gene therapies in low- and middle-income countries.
Sci Transl Med
; 16(746): eadn1902, 2024 May 08.
Artigo
Inglês
| MEDLINE | ID: mdl-38718130
17.
Hematopoietic stem/progenitor cells, generation of induced pluripotent stem cells, and isolation of endothelial progenitors from 21- to 23.5-year cryopreserved cord blood.
Blood
; 117(18): 4773-7, 2011 May 05.
Artigo
Inglês
| MEDLINE | ID: mdl-21393480
18.
Transgenic sheep generated by lentiviral vectors: safety and integration analysis of surrogates and their offspring.
Transgenic Res
; 22(4): 737-45, 2013 Aug.
Artigo
Inglês
| MEDLINE | ID: mdl-23180364
19.
Meeting FDA Guidance recommendations for replication-competent virus and insertional oncogenesis testing.
Mol Ther Methods Clin Dev
; 28: 28-39, 2023 Mar 09.
Artigo
Inglês
| MEDLINE | ID: mdl-36588821
20.
Telehospice for Cancer Patients Discharged from a Tertiary Care Hospital in Western Kenya.
J Pain Symptom Manage
; 65(5): 378-387, 2023 05.
Artigo
Inglês
| MEDLINE | ID: mdl-36773732