Detalhe da pesquisa
1.
Risk factors associated with prevalent vertebral fractures in Duchenne muscular dystrophy.
Osteoporos Int
; 34(1): 147-160, 2023 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-36342539
2.
Serum biomarkers associated with baseline clinical severity in young steroid-naïve Duchenne muscular dystrophy boys.
Hum Mol Genet
; 29(15): 2481-2495, 2020 08 29.
Artigo
Inglês
| MEDLINE | ID: mdl-32592467
3.
Optimization of DOTAP/chol Cationic Lipid Nanoparticles for mRNA, pDNA, and Oligonucleotide Delivery.
AAPS PharmSciTech
; 23(5): 135, 2022 May 09.
Artigo
Inglês
| MEDLINE | ID: mdl-35534697
4.
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study.
PLoS Med
; 17(9): e1003222, 2020 09.
Artigo
Inglês
| MEDLINE | ID: mdl-32956407
5.
Phenethyl Isothiocyanate and Cisplatin Co-Encapsulated in a Liposomal Nanoparticle for Treatment of Non-Small Cell Lung Cancer.
Molecules
; 24(4)2019 Feb 22.
Artigo
Inglês
| MEDLINE | ID: mdl-30813352
6.
Divergent subgenome evolution after allopolyploidization in African clawed frogs (Xenopus).
J Evol Biol
; 31(12): 1945-1958, 2018 12.
Artigo
Inglês
| MEDLINE | ID: mdl-30341989
7.
markophylo: Markov chain analysis on phylogenetic trees.
Bioinformatics
; 32(1): 130-2, 2016 Jan 01.
Artigo
Inglês
| MEDLINE | ID: mdl-26363176
8.
Mixtures of multivariate power exponential distributions.
Biometrics
; 71(4): 1081-9, 2015 Dec.
Artigo
Inglês
| MEDLINE | ID: mdl-26134429
9.
Assessing Pharmacogenomic loci Associated with the Pharmacokinetics of Vamorolone in Boys with Duchenne Muscular Dystrophy.
J Clin Pharmacol
; 2024 Apr 29.
Artigo
Inglês
| MEDLINE | ID: mdl-38682893
10.
Findings from the Longitudinal CINRG Becker Natural History Study.
J Neuromuscul Dis
; 11(1): 201-212, 2024.
Artigo
Inglês
| MEDLINE | ID: mdl-37980682
11.
Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy: A Randomized Controlled Trial.
Neurology
; 102(5): e208112, 2024 Mar 12.
Artigo
Inglês
| MEDLINE | ID: mdl-38335499
12.
Modeling Early Heterogeneous Rates of Progression in Boys with Duchenne Muscular Dystrophy.
J Neuromuscul Dis
; 10(3): 349-364, 2023.
Artigo
Inglês
| MEDLINE | ID: mdl-36806514
13.
Acute serum protein and cytokine response of single dose of prednisone in adult volunteers.
Steroids
; 178: 108953, 2022 02.
Artigo
Inglês
| MEDLINE | ID: mdl-35026285
14.
Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial.
JAMA Netw Open
; 5(1): e2144178, 2022 01 04.
Artigo
Inglês
| MEDLINE | ID: mdl-35076703
15.
Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial.
JAMA Neurol
; 79(10): 1005-1014, 2022 10 01.
Artigo
Inglês
| MEDLINE | ID: mdl-36036925
16.
Biomarker-focused multi-drug combination therapy and repurposing trial in mdx mice.
PLoS One
; 16(2): e0246507, 2021.
Artigo
Inglês
| MEDLINE | ID: mdl-33617542
17.
Interrogation of Dystrophin and Dystroglycan Complex Protein Turnover After Exon Skipping Therapy.
J Neuromuscul Dis
; 8(s2): S383-S402, 2021.
Artigo
Inglês
| MEDLINE | ID: mdl-34569969
18.
Validation of Chemokine Biomarkers in Duchenne Muscular Dystrophy.
Life (Basel)
; 11(8)2021 Aug 13.
Artigo
Inglês
| MEDLINE | ID: mdl-34440571
19.
Serum protein biomarkers for juvenile dermatomyositis: a pilot study.
BMC Rheumatol
; 4: 52, 2020.
Artigo
Inglês
| MEDLINE | ID: mdl-33015544
20.
Comparison of Serum Pharmacodynamic Biomarkers in Prednisone-Versus Deflazacort-Treated Duchenne Muscular Dystrophy Boys.
J Pers Med
; 10(4)2020 Oct 12.
Artigo
Inglês
| MEDLINE | ID: mdl-33053810