Detalhe da pesquisa
1.
Post-Transcriptional Genetic Silencing of BCL11A to Treat Sickle Cell Disease.
N Engl J Med
; 384(3): 205-215, 2021 01 21.
Artigo
Inglês
| MEDLINE | ID: mdl-33283990
2.
Bidirectional processes linking social determinants of health and pediatric sickle cell anemia management: A qualitative study.
Pediatr Blood Cancer
; 70(10): e30539, 2023 10.
Artigo
Inglês
| MEDLINE | ID: mdl-37470711
3.
Inactivation of HDAC1 or HDAC2 induces gamma globin expression without altering cell cycle or proliferation.
Am J Hematol
; 90(7): 624-8, 2015 Jul.
Artigo
Inglês
| MEDLINE | ID: mdl-25808664
4.
Clonal selection of hematopoietic stem cells after gene therapy for sickle cell disease.
Nat Med
; 29(12): 3175-3183, 2023 Dec.
Artigo
Inglês
| MEDLINE | ID: mdl-37973947
5.
Genetic reversal of the globin switch concurrently modulates both fetal and sickle hemoglobin and reduces red cell sickling.
Nat Commun
; 14(1): 5850, 2023 09 20.
Artigo
Inglês
| MEDLINE | ID: mdl-37730674
6.
Secondary Neoplasms After Hematopoietic Cell Transplant for Sickle Cell Disease.
J Clin Oncol
; 41(12): 2227-2237, 2023 04 20.
Artigo
Inglês
| MEDLINE | ID: mdl-36623245
7.
Phase 1/2 trial of vorinostat in patients with sickle cell disease who have not benefitted from hydroxyurea.
Blood
; 125(23): 3668-9, 2015 Jun 04.
Artigo
Inglês
| MEDLINE | ID: mdl-26045597
8.
ß-Thalassemia: evolving treatment options beyond transfusion and iron chelation.
Hematology Am Soc Hematol Educ Program
; 2021(1): 600-606, 2021 12 10.
Artigo
Inglês
| MEDLINE | ID: mdl-34889443
9.
Highly efficient therapeutic gene editing of human hematopoietic stem cells.
Nat Med
; 25(5): 776-783, 2019 05.
Artigo
Inglês
| MEDLINE | ID: mdl-30911135
10.
Genetic therapies for sickle cell disease.
Semin Hematol
; 55(2): 76-86, 2018 04.
Artigo
Inglês
| MEDLINE | ID: mdl-29958563
11.
Successful hematopoietic stem cell mobilization and apheresis collection using plerixafor alone in sickle cell patients.
Blood Adv
; 2(19): 2505-2512, 2018 10 09.
Artigo
Inglês
| MEDLINE | ID: mdl-30282642
12.
Correction of sickle cell disease in adult mice by interference with fetal hemoglobin silencing.
Science
; 334(6058): 993-6, 2011 Nov 18.
Artigo
Inglês
| MEDLINE | ID: mdl-21998251