Detalhe da pesquisa
1.
AAV-Mediated Delivery of Plakophilin-2a Arrests Progression of Arrhythmogenic Right Ventricular Cardiomyopathy in Murine Hearts: Preclinical Evidence Supporting Gene Therapy in Humans.
Circ Genom Precis Med
; 17(1): e004305, 2024 Feb.
Artigo
Inglês
| MEDLINE | ID: mdl-38288614
2.
Genetic Modification of the AAV5 Capsid with Lysine Residues Results in a Lung-Tropic Liver-Detargeted Gene Transfer Vector.
Hum Gene Ther
; 33(3-4): 148-154, 2022 02.
Artigo
Inglês
| MEDLINE | ID: mdl-35018834
3.
Gene therapy for alpha 1-antitrypsin deficiency with an oxidant-resistant human alpha 1-antitrypsin.
JCI Insight
; 5(15)2020 08 06.
Artigo
Inglês
| MEDLINE | ID: mdl-32759494
4.
Gene Therapy Correction of Aldehyde Dehydrogenase 2 Deficiency.
Mol Ther Methods Clin Dev
; 15: 72-82, 2019 Dec 13.
Artigo
Inglês
| MEDLINE | ID: mdl-31649957
5.
Genetic modification of neurons to express bevacizumab for local anti-angiogenesis treatment of glioblastoma.
Cancer Gene Ther
; 22(1): 1-8, 2015 Jan.
Artigo
Inglês
| MEDLINE | ID: mdl-25501993
6.
Intrapleural administration of an AAVrh.10 vector coding for human α1-antitrypsin for the treatment of α1-antitrypsin deficiency.
Hum Gene Ther Clin Dev
; 24(4): 161-73, 2013 Dec.
Artigo
Inglês
| MEDLINE | ID: mdl-24191907
7.
Membrane-bound SIV envelope trimers are immunogenic in ferrets after intranasal vaccination with a replication-competent canine distemper virus vector.
Virology
; 446(1-2): 25-36, 2013 Nov.
Artigo
Inglês
| MEDLINE | ID: mdl-24074564
8.
AAVrh.10-mediated expression of an anti-cocaine antibody mediates persistent passive immunization that suppresses cocaine-induced behavior.
Hum Gene Ther
; 23(5): 451-9, 2012 May.
Artigo
Inglês
| MEDLINE | ID: mdl-22486244