Detalhe da pesquisa
1.
Base-Edited CAR7 T Cells for Relapsed T-Cell Acute Lymphoblastic Leukemia.
N Engl J Med
; 389(10): 899-910, 2023 Sep 07.
Artigo
Inglês
| MEDLINE | ID: mdl-37314354
2.
Clinically Applicable Assessment of Tisagenlecleucel CAR T Cell Treatment by Digital Droplet PCR for Copy Number Variant Assessment.
Int J Mol Sci
; 23(14)2022 Jul 08.
Artigo
Inglês
| MEDLINE | ID: mdl-35886920
3.
'Mini' U6 Pol III promoter exhibits nucleosome redundancy and supports multiplexed coupling of CRISPR/Cas9 effects.
Gene Ther
; 27(9): 451-458, 2020 09.
Artigo
Inglês
| MEDLINE | ID: mdl-32203198
4.
Cytosine Deaminase Base Editing to Restore COL7A1 in Dystrophic Epidermolysis Bullosa Human: Murine Skin Model.
JID Innov
; 3(3): 100191, 2023 May.
Artigo
Inglês
| MEDLINE | ID: mdl-37213713
5.
Phase 1 clinical trial of CRISPR-engineered CAR19 universal T cells for treatment of children with refractory B cell leukemia.
Sci Transl Med
; 14(668): eabq3010, 2022 10 26.
Artigo
Inglês
| MEDLINE | ID: mdl-36288281
6.
Base-edited CAR T cells for combinational therapy against T cell malignancies.
Leukemia
; 35(12): 3466-3481, 2021 12.
Artigo
Inglês
| MEDLINE | ID: mdl-34035409
7.
CRISPR-Mediated Base Conversion Allows Discriminatory Depletion of Endogenous T Cell Receptors for Enhanced Synthetic Immunity.
Mol Ther Methods Clin Dev
; 19: 149-161, 2020 Dec 11.
Artigo
Inglês
| MEDLINE | ID: mdl-33102612
8.
Quantifying CRISPR off-target effects.
Emerg Top Life Sci
; 3(3): 327-334, 2019 May 31.
Artigo
Inglês
| MEDLINE | ID: mdl-33523136
9.
Striking phenotypic variation in a family with the P506S UBQLN2 mutation including amyotrophic lateral sclerosis, spastic paraplegia, and frontotemporal dementia.
Neurobiol Aging
; 73: 229.e5-229.e9, 2019 01.
Artigo
Inglês
| MEDLINE | ID: mdl-30348461